Inherited Retinal Dystrophy Due to RPE65 Mutations
Drug | Drug Name | Drug Description |
---|
Drug | Drug Name | Target | Type |
---|
Drug | Drug Name | Phase | Status | Count |
---|---|---|---|---|
DB13932 | Voretigene neparvovec | 3 | Active Not Recruiting | 1 |
DB13932 | Voretigene neparvovec | Not Available | Active Not Recruiting | 1 |