Aromatic L-amino Acid Decarboxylase (AADC) Deficiency
Also known as: Aromatic Amino Acid Decarboxylase Deficiency / AADC Deficiency / Aromatic L-amino Acid Decarboxylase Deficiency / Deficiency of aromatic-L-amino-acid decarboxylase (disorder) / Aromatic amino acid decarboxylase deficiency (disorder)
| Drug | Drug Name | Drug Description |
|---|---|---|
| DB16780 | Eladocagene exuparvovec | A recombinant AAV2 vector containing the human aromatic L-amino acid decarboxylase (AADC) gene indicated for the treatment of AADC deficiency. |
| Drug | Drug Name | Target | Type |
|---|
| Drug | Drug Name | Phase | Status | Count |
|---|---|---|---|---|
| DB09393 | Amino acids | 1 | Recruiting | 1 |
| DB16780 | Eladocagene exuparvovec | 1 / 2 | Completed | 1 |