Neurologic Dysfunction

DrugDrug NameDrug Description
DB16746Elivaldogene autotemcelA gene replacement therapy for treating early cerebral adrenoleukodystrophy comprising autologous hematopoietic stem cells transduced with a viral vector encoding ABCD1 complementary DNA for human adrenoleukodystrophy protein.
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount