Confirmed Biallelic RPE65 Mutation-associated Retinal Dystrophy
Drug | Drug Name | Drug Description |
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Drug | Drug Name | Target | Type |
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Drug | Drug Name | Phase | Status | Count |
---|---|---|---|---|
DB13932 | Voretigene neparvovec | Not Available | Active Not Recruiting | 1 |
Drug | Drug Name | Drug Description |
---|
Drug | Drug Name | Target | Type |
---|
Drug | Drug Name | Phase | Status | Count |
---|---|---|---|---|
DB13932 | Voretigene neparvovec | Not Available | Active Not Recruiting | 1 |