Amyotrophic Lateral Sclerosis Associated With a SOD1 Gene Mutation

Also known as: Superoxide Dismutase 1-Amyotropic Lateral Sclerosis / ALS Caused by Superoxide Dismutase 1 (SOD1) Mutation

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB14782Tofersen3Active Not Recruiting1
DB14782Tofersen3Recruiting1
DB14782TofersenNot AvailableApproved for Marketing1