Usher Syndrome Type 2 (DBCOND0056060)

Identifiers

Synonyms

Usher syndrome type 2 / Usher syndrome type 2 (disorder)

Associated Data

Indicated Drugs and Targets

Not Available

Clinical Trials

Identifier	Title	Drug(s)	Purpose	Phase	Status
NCT06627179	Study to Evaluate Ultevursen in Subjects with Retinitis Pigmentosa (RP) Due to Mutations in Exon 13 of the USH2A Gene	Ultevursen	treatment	2	not_yet_recruiting
NCT05085964	An Open-Label Extension Study to Evaluate Safety & Tolerability of QR-421a in Subjects With Retinitis Pigmentosa	Ultevursen	treatment	2	terminated
NCT01530659	Retinal Imaging in CNTF -Releasing Encapsulated Cell Implant Treated Patients for Early-stage Retinitis Pigmentosa	Ciliary neurotrophic factor	treatment	2	completed
NCT05176717	Study to Evaluate the Efficacy Safety and Tolerability of QR-421a in Subjects With RP Due to Mutations in Exon 13 of the USH2A Gene With Early to Moderate Vision Loss (Celeste)	Ultevursen	treatment	2 / 3	terminated
NCT05158296	Study to Evaluate the Efficacy Safety and Tolerability of Ultevursen in Subjects With RP Due to Mutations in Exon 13 of the USH2A Gene (Sirius)	Ultevursen	treatment	2 / 3	terminated
NCT03780257	Study to Evaluate Safety and Tolerability of QR-421a in Subjects With RP Due to Mutations in Exon 13 of the USH2A Gene	Ultevursen	treatment	1 / 2	completed