Polyneuropathies caused by Hereditary transthyretin-mediated amyloidosis (DBCOND0126276)

Identifiers

Synonyms
Not Available

Associated Data

Indicated Drugs and Targets
DrugDescriptionTargets
Eplontersen
A transthyretin antisense oligonucleotide used to treat polyneuropathy of hereditary transthyretin-mediated amyloidosis.
Inotersen
An antisense oligonucleotide used to treat polyneuropathy of hereditary transthyretin-mediated amyloidosis.
Clinical Trials
Not Available