Polyneuropathies caused by Hereditary transthyretin-mediated amyloidosis (DBCOND0126276)
Identifiers
- Synonyms
- Not Available
Associated Data
- Indicated Drugs and Targets
Drug Description Targets Eplontersen A transthyretin antisense oligonucleotide used to treat polyneuropathy of hereditary transthyretin-mediated amyloidosis.- Transthyretin mRNAtarget
Inotersen An antisense oligonucleotide used to treat polyneuropathy of hereditary transthyretin-mediated amyloidosis.- Transthyretin mRNAtarget
- Transthyretintarget
- Clinical Trials
- Not Available