Hereditary Transthyretin Amyloidosis (DBCOND0133633)

Identifiers

Synonyms

Hereditary transthyretin amyloidosis

Associated Data

Indicated Drugs and Targets

Drug	Description	Targets
Inotersen	An antisense oligonucleotide used to treat polyneuropathy of hereditary transthyretin-mediated amyloidosis.	Transthyretin mRNAtarget Transthyretintarget

Clinical Trials

Identifier	Title	Drug(s)	Purpose	Phase	Status
NCT05929209	Exploring Biomarkers in Hereditary Transthyretin Amyloidosis	No drug interventions	diagnostic	Not Available	recruiting
NCT06414746	Hereditary Transthyretin Amyloidosis Polyneuropathy in Patients With Carpal Tunnel Syndrome in Russia	No drug interventions	Not Available	Not Available	recruiting
NCT06365593	hATTR Polyneuropathy in Russia	No drug interventions	Not Available	Not Available	completed