Type 2 Gaucher Disease

Also known as: Type II Gaucher Disease / Gaucher's disease type II / Gaucher Disease, Type II / Gaucher Disease, Type 2 / Acute neuronopathic Gaucher's disease (disorder)

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB01272Alglucosidase alfa1Recruiting1
DB09051Elosulfase alfa1Recruiting1
DB01279Galsulfase1Recruiting1
DB01271Idursulfase1Recruiting1
DB00090Laronidase1Recruiting1
DB11563Sebelipase alfa1Recruiting1
DB12366Vestronidase alfa1Recruiting1
DB00959Methylprednisolone1 / 2Active Not Recruiting1
DB00635Prednisone1 / 2Active Not Recruiting1
DB00877Sirolimus1 / 2Active Not Recruiting1