BH4 Deficiency

Also known as: Tetrahydrobiopterin synthesis defect (disorder) / Hyperphenylalaninemia, Non-Phenylketonuric / Tetrahydrobiopterin deficiency

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB16326Sepiapterin1 / 2Completed1