Glycogen Storage Disease Type II Infantile Onset

Also known as: Glycogen storage disease type II infantile onset (disorder) / Pompe's disease infantile onset

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB16708Cipaglucosidase alfa3Recruiting1
DB00419Miglustat3Recruiting1