Displaying drugs 15251 - 15275 of 15606 in total
RGX-181
RGX-181 consists of an adeno-associated virus serotype 9 (AAV9) vector designed to deliver the soluble lysosomal enzyme tripeptidyl peptidase I (TPP1) gene. Developed by REGENXBIO, it is being investigated for the treatment of late-infantile neuronal ceroid lipofuscinosis type 2 (CLN2) disease.
Investigational
AVXS-301
AVXS-301 consists of an adeno-associated virus serotype 9 (AAV9) designed to express the superoxide dismutase 1 (SOD1) gene. It is being investigated for the treatment of Amyotrophic Lateral Sclerosis (ALS).
Investigational
HER-902
Investigational
CNM-Au8
Investigational
Human Embryonic Stem Cell-derived Astrocytes
Investigational
GALE-302
Investigational
ISIS-333611
Investigational
Recombinant human palmitoyl protein thioesterase-1
Investigational
Baloramotide
Investigational
PLX-R18
Investigational
SGN-1
SGN-1 is a genetically modified strain of Salmonella enterica comprising methioninase.
Investigational
Alidornase alfa
Investigational
CLBS12
CLBS12 is a GCSF-mobilized autologous cell therapy derived from CD34+ cells being investigated for the treatment of Buerger’s disease.
Investigational
Eneboparatide
Investigational
Gresonitamab
Investigational
Vepsitamab
Investigational
Haptoglobulin 1/1 (Plasma Derived)
Investigational
KB407
Investigational
Belcesiran
Investigational
SPK-7001
Investigational
M012
Investigational
Nadunolimab
Investigational
OAV401
Investigational
Displaying drugs 15251 - 15275 of 15606 in total