D-Bifunctional Protein Deficiency (DBCOND0126800)
Identifiers
- Synonyms
- D-Bifunctional Enzyme Deficiency / Bifunctional Enzyme Deficiency
Associated Data
- Indicated Drugs and Targets
- Not Available
- Clinical Trials
Identifier Title Drug(s) Purpose Phase Status NCT02171104 MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis No drug interventions treatment 2 recruiting NCT01668186 Longitudinal Natural History Study of Patients With Peroxisome Biogenesis Disorders (PBD) No drug interventions Not Available Not Available recruiting NCT00004442 Study of Bile Acids in Patients With Peroxisomal Disorders treatment Not Available terminated