Severe Hemophilia A
Also known as: Severe Haemophilia A / Hemophilia A, Severe
Drug | Drug Name | Drug Description |
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DB15561 | Valoctocogene roxaparvovec | An adeno-associated virus serotype 5 (AAV5)-based gene therapy containing a coagulation factor VIII complementary DNA used to treat severe hemophilia A. |
Drug | Drug Name | Target | Type |
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