Severe Hemophilia A

Also known as: Severe Haemophilia A / Hemophilia A, Severe

DrugDrug NameDrug Description
DB15561Valoctocogene roxaparvovecAn adeno-associated virus serotype 5 (AAV5)-based gene therapy containing a coagulation factor VIII complementary DNA used to treat severe hemophilia A.
DrugDrug NameTargetType