Late-onset Pompe Disease
Also known as: Late Onset Pompe Disease / Pompe Disease Late-Onset / Pompe Disease (Late-Onset)
| Drug | Drug Name | Drug Description |
|---|---|---|
| DB16099 | Avalglucosidase alfa | A lysosomal glycogen-specific enzyme that is used to treat patients one year of age and older with late-onset Pompe disease, or lysosomal acid alpha-glucosidase (GAA) deficiency. |
| Drug | Drug Name | Target | Type |
|---|---|---|---|
| DB16099 | Avalglucosidase alfa | Cation-independent mannose-6-phosphate receptor | target |
| Drug | Drug Name | Phase | Status | Count |
|---|---|---|---|---|
| DB01272 | Alglucosidase alfa | 2 | Completed | 2 |
| DB01407 | Clenbuterol | 2 | Withdrawn | 1 |
| DB01272 | Alglucosidase alfa | 3 | Completed | 3 |
| DB16708 | Cipaglucosidase alfa | 3 | Active Not Recruiting | 1 |
| DB16708 | Cipaglucosidase alfa | 3 | Completed | 1 |
| DB16708 | Cipaglucosidase alfa | 3 | Recruiting | 1 |
| DB00419 | Miglustat | 3 | Active Not Recruiting | 1 |
| DB00419 | Miglustat | 3 | Completed | 1 |
| DB00419 | Miglustat | 3 | Recruiting | 1 |
| DB01272 | Alglucosidase alfa | 4 | Completed | 2 |
| DB01272 | Alglucosidase alfa | Not Available | Approved for Marketing | 1 |
| DB01272 | Alglucosidase alfa | Not Available | Unknown Status | 1 |