Pyruvate Dehydrogenase Complex Deficiency

Also known as: Pyruvate Dehydrogenase Complex Deficiency Disease / Disorders of pyruvate metabolism and gluconeogenesis / Pyruvate dehydrogenase deficiency / Pyruvate dehydrogenase complex deficiency (disorder) / Deficiency of pyruvic dehydrogenase / Deficiency of pyruvate decarboxylase (disorder)

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB06819Phenylbutyric acid2Completed1
DB08809Dichloroacetic acid3Active Not Recruiting1
DB16929Sodium dichloroacetate3Active Not Recruiting1