Displaying drugs 14876 - 14900 of 15371 in total
PTR-01
Investigational
rAAVrh74.MCK.GALGT2
Investigational
Nomlabofusp
Investigational
Autologous adipose derived mesenchymal stromal cells
Investigational
Autologous cord blood
Investigational
INT41
INT41 (also known as rAAV6-INT41) is a recombinant adeno-associated virus vector containing DNA encoding INT41 intrabody.
Investigational
RGX-181
RGX-181 consists of an adeno-associated virus serotype 9 (AAV9) vector designed to deliver the soluble lysosomal enzyme tripeptidyl peptidase I (TPP1) gene. Developed by REGENXBIO, it is being investigated for the treatment of late-infantile neuronal ceroid lipofuscinosis type 2 (CLN2) disease.
Investigational
AVXS-301
AVXS-301 consists of an adeno-associated virus serotype 9 (AAV9) designed to express the superoxide dismutase 1 (SOD1) gene. It is being investigated for the treatment of Amyotrophic Lateral Sclerosis (ALS).
Investigational
HER-902
Investigational
CNM-Au8
Investigational
Human Embryonic Stem Cell-derived Astrocytes
Investigational
GALE-302
Investigational
C-Alpha-stx2
Investigational
ISIS-333611
Investigational
Recombinant human palmitoyl protein thioesterase-1
Investigational
Baloramotide
Investigational
PLX-R18
Investigational
SGN-1
SGN-1 is a genetically modified strain of Salmonella enterica comprising methioninase.
Investigational
Briquilimab
Briquilimab is a humanized aglycosylated IgG1 kappa monoclonal antibody targeting CD117 (cKit).
Investigational
Alidornase alfa
Investigational
Nemvaleukin alfa
Investigational
CLBS12
CLBS12 is a GCSF-mobilized autologous cell therapy derived from CD34+ cells being investigated for the treatment of Buerger’s disease.
Investigational
Displaying drugs 14876 - 14900 of 15371 in total