Aceneuramic acid

DB11797InvestigationalSmall molecule

Aceneuramic acid has been used in trials studying the treatment of Distal Myopathy, Nonaka Type, Hereditary Inclusion Body Myopathy, and Distal Myopathy With Rimmed Vacuoles.

Formula / weight: C₁₁H₁₉NO₉ · 309.2699 g/mol (avg)
Code names: NPC-09 · UX-001

Resolves to

Compound

UNIIGZP2782OP0CAS131-48-6ChEMBLCHEMBL2105945PubChem14017587

Clinical / RWD

RxNorm2613558ATCM09AX05

Structure

InChIKeyKBGAYAKRZNYFFG-BOHATCBPSA-NSMILESCC(=O)N[C@H]([C@@H](O)CC(=O)C(O)=O)[C@@H](O)[C@H](O)[C@H](O)CO

Targets

Q9Y223GNE

What you can answer from here — as of July 07, 2026

1Protein targetEach mapped to UniProt, with action and pharmacological action

Listed above

5Clinical trialsPhase, status and sponsor resolved per trial

1ATC codeIncluding every combination product, plus 1 drug category

3+ReferencesStructured and connected to the statements they support

Which drugs share a target with Aceneuramic acid, and which of those have an active Phase 3 trial?

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