Hurlers Syndrome

Also known as: Hurler's Syndrome / Hurler Syndrome / Dysostosis multiplex (disorder) / Mucopolysaccharidosis, MPS-I (disorder) / MPS I H / (Mucopolysaccharidosis: (& [gargoylism]/[Hunter][Hurler]/[lipochondrodyst]/[Maroteaux-Lamy]/[Morquio-Brailsford]/[osteochondrodystrophy]/[Sanfilippo]/[Scheie]) or (dysostos multi) / Mucopolysaccharidosis, MPS-I-H (disorder) / Hurler's disease / Mucopolysaccharidosis, type 1: (& [gargoylism] or [Hurler's syndrome] or [Scheie's syndrome]) / Mucopolysaccharidosis I / Mucopolysaccharidosis type I [Ambiguous] / Mucopolysaccharidosis, type I

DrugDrug NameDrug Description
DB00090LaronidaseA form of recombinant human alpha-L-iduronidase used to treat Hurler and Hurler-Scheie forms of mucopolysaccharidosis, a genetic deficiency of alpha-L-iduronidase.
DrugDrug NameTargetType
DB00090LaronidaseIduronic acidtarget
DrugDrug NamePhaseStatusCount
DB01281Abatacept1Completed1
DB00090Laronidase1Completed2
DB04572Thiotepa1 / 2Recruiting1
DB00087Alemtuzumab2Completed1
DB00087Alemtuzumab2Terminated1
DB01008Busulfan2Completed1
DB01008Busulfan2Terminated1
DB00531Cyclophosphamide2Completed1
DB00531Cyclophosphamide2Terminated1
DB00091Cyclosporine2Completed1
DB00090Laronidase2Completed2
DB00688Mycophenolate mofetil2Completed1
DB00090Laronidase3Completed3
DB11105Benzalkonium4Recruiting1
DB00090Laronidase4Completed2
DB00090Laronidase4Recruiting1
DB00090LaronidaseNot AvailableTerminated1
DB04974RimiducidNot AvailableNo Longer Available1
DB00052SomatotropinNot AvailableWithdrawn1