Mucopolysaccharidosis Type I (MPS I)

Also known as: Mucopolysaccharidosis Type 1 / Mucopolysaccharidosis IS / Mucopolysaccharidosis I / Mucopolysaccharidosis Type I / Type 1 Mucopolysaccharidosis / Scheie's syndrome / Mucopolysaccharidosis V / Scheie Syndrome / Mucopolysaccharidosis, MPS-I-S (disorder) / Mucopolysaccharidosis, type I / Mucopolysaccharidosis, MPS-I (disorder)

DrugDrug NameDrug Description
DB00090LaronidaseA form of recombinant human alpha-L-iduronidase used to treat Hurler and Hurler-Scheie forms of mucopolysaccharidosis, a genetic deficiency of alpha-L-iduronidase.
DrugDrug NameTargetType
DB00090LaronidaseIduronic acidtarget
DrugDrug NamePhaseStatusCount
DB11105Benzalkonium1Completed2
DB00030Insulin human1Completed2
DB00090Laronidase1Terminated2
DB15336Valanafusp alfa1Completed2
DB00051Adalimumab1 / 2Active Not Recruiting1
DB00051Adalimumab1 / 2Completed1
DB00993Azathioprine1 / 2Completed1
DB00091Cyclosporine1 / 2Completed1
DB00090Laronidase1 / 2Completed1
DB19011Lepunafusp alfa1 / 2Active Not Recruiting1
DB19011Lepunafusp alfa1 / 2Completed1
DB15336Valanafusp alfa1 / 2Completed2
DB00098Antithymocyte immunoglobulin (rabbit)2Completed1
DB01008Busulfan2Completed1
DB00531Cyclophosphamide2Completed1
DB00090Laronidase2Completed2
DB00052Somatotropin2 / 3Terminated1
DB00090Laronidase3Completed4
DB11105Benzalkonium4Terminated1
DB00090Laronidase4Completed3
DB00090Laronidase4Terminated1
DB16788Adlinacogene civaparvovecNot AvailableActive Not Recruiting1
DB11105BenzalkoniumNot AvailableTerminated1
DB16790Devafidugene civaparvovecNot AvailableActive Not Recruiting1
DB00090LaronidaseNot AvailableCompleted1
DB00090LaronidaseNot AvailableRecruiting1
DB00090LaronidaseNot AvailableTerminated1
DB16789Tefidsogene civaparvovecNot AvailableActive Not Recruiting1