Dyskeratosis Congenita (DBCOND0002529)
Identifiers
- Synonyms
- Congenital dyskeratosis / Dyskeratosis-congenita / Dyskeratosis congenita / Dyskeratosis congenita (disorder)
Associated Data
- Indicated Drugs and Targets
- Not Available
- Clinical Trials
Identifier Title Drug(s) Purpose Phase Status NCT01319851 Alefacept and Allogeneic Hematopoietic Stem Cell Transplantation treatment Not Available terminated NCT01917708 Bone Marrow Transplant With Abatacept for Non-Malignant Diseases supportive_care 1 completed NCT00027274 Cancer in Inherited Bone Marrow Failure Syndromes No drug interventions Not Available Not Available recruiting NCT04959188 Needs Assessment for Individuals and Families Affected by Dyskeratosis Congenita (DC) and Related Telomere Biology Disorders (TBD) No drug interventions Not Available Not Available completed NCT02720679 Investigation of the Genetics of Hematologic Diseases No drug interventions Not Available Not Available recruiting NCT01001598 Safety and Efficacy Trial of Danazol in Patients With Fanconi Anemia or Dyskeratosis Congenita treatment 1 / 2 terminated NCT03579875 Alpha/Beta TCD HCT in Patients With Inherited BMF Disorders treatment 2 recruiting NCT00499070 Assessing Immune Function in Young Patients With Cytopenia That Did Not Respond to Treatment No drug interventions Not Available Not Available completed NCT01659606 Radiation- and Alkylator-free Bone Marrow Transplantation Regimen for Patients With Dyskeratosis Congenita treatment 2 active_not_recruiting NCT04638517 The TELO-SCOPE Study: Attenuating Telomere Attrition With Danazol. Is There Scope to Dramatically Improve Health Outcomes for Adults and Children With Pulmonary Fibrosis treatment 2 recruiting NCT00004787 Phase II Pilot Study of Granulocyte Colony-Stimulating Factor for Inherited Bone Marrow Failure Syndromes treatment 2 completed NCT02162420 Hematopoietic Stem Cell Transplant for Dyskeratosis Congenita or Severe Aplastic Anemia treatment Not Available active_not_recruiting NCT03050268 Familial Investigations of Childhood Cancer Predisposition No drug interventions Not Available Not Available recruiting NCT00455312 Stem Cell Transplant (SCT) for Dyskeratosis Congenita or SAA treatment 2 / 3 completed