Wiskott-Aldrich Syndrome (WAS) (DBCOND0042107)

Identifiers

Synonyms
Wiskott- Aldrich Syndrome / Wiskott-Aldrich Syndrome / Aldrich syndrome / Wiskott-Aldrich syndrome (disorder)

Associated Data

Indicated Drugs and Targets
Not Available
Clinical Trials
IdentifierTitleDrug(s)PurposePhaseStatus
NCT00579137
Allogeneic SCT Of Pts With SCID And Other Primary Immunodeficiency Disorderstreatment1 / 2terminated
NCT00006319
Molecular and Clinical Studies of Primary Immunodeficiency DiseasesNo drug interventionsNot AvailableNot Availableactive_not_recruiting
NCT01515462
Gene Therapy for Wiskott-Aldrich SyndromeNo drug interventionstreatment1 / 2completed
NCT00774358
Interleukin-2 Treatment for Wiskott-Aldrich Syndrometreatment1completed
NCT02512679
Related Hematopoietic Stem Cell Transplantation (HSCT) for Genetic Diseases of Blood Cellstreatment2terminated
NCT02064933
Patients Treated for Wiskott-Aldrich Syndrome (WAS) Since 1990No drug interventionsNot AvailableNot Availablecompleted
NCT00006054
Allogeneic Bone Marrow Transplantation in Patients With Primary ImmunodeficienciestreatmentNot Availableterminated
NCT01319851
Alefacept and Allogeneic Hematopoietic Stem Cell TransplantationtreatmentNot Availableterminated
NCT03019809
A Trial of Plerixafor/G-CSF as Additional Agents for Conditioning Before TCR Alpha/Beta Depleted HSCT in WAS Patientstreatment2unknown_status
NCT01347242
Gene Therapy for Wiskott-Aldrich Syndrome (WAS)No drug interventionstreatment1 / 2completed
NCT03333486
Fludarabine Phosphate, Cyclophosphamide, Total Body Irradiation, and Donor Stem Cell Transplant in Treating Patients With Blood Cancertreatment2active_not_recruiting
NCT04371939
Efficacy and Safety of Romiplostim Versus Eltrombopag in the Treatment of Thrombocytopenia in Patients With Wiskott-Aldrich Syndrometreatment2unknown_status
NCT01410825
Pilot and Feasibility Study of Hematopoietic Stem Cell Gene Transfer for the Wiskott-Aldrich SyndromeNo drug interventionstreatment1 / 2active_not_recruiting
NCT01529827
Fludarabine Phosphate, Melphalan, and Low-Dose Total-Body Irradiation Followed by Donor Peripheral Blood Stem Cell Transplant in Treating Patients With Hematologic Malignanciestreatment2completed
NCT02333760
Long Term Safety Follow up of Haematopoietic Stem Cell Gene Therapy for the Wiskott Aldrich SyndromeNo drug interventionsother1 / 2active_not_recruiting
NCT01652092
Allogeneic Hematopoietic Stem Cell Transplant for Patients With Primary Immune DeficienciestreatmentNot Availablerecruiting
NCT01347346
Gene Therapy for WASNo drug interventionstreatment1 / 2completed
NCT01821781
Immune Disorder HSCT Protocoltreatment2recruiting
NCT00730314
Unrelated Hematopoietic Stem Cell Transplantation(HSCT) for Genetic Diseases of Blood CellsNo drug interventionstreatment1 / 2completed
NCT04350164
Romiplostim Treatment for Thrombocytopenia in Patients With Wiskott-Aldrich Syndrome.Not AvailableNot Availablecompleted
NCT00885833
Study of Reduced Toxicity Myeloablative Conditioning Regimen for Wiskott-Aldrich Syndrome (WAS)treatment1 / 2completed
NCT00278954
Efficacy, Safety and Pharmacokinetics of Gammaplex in Primary Immunodeficiency Diseases.treatment3completed
NCT01289847
A Study to Find Out How Safe and Effective Gammaplex® is in Young People With Primary Immunodeficiencyprevention4completed
NCT03837483
A Clinical Study to Evaluate the Use of a Cryopreserved Formulation of OTL-103 in Subjects With Wiskott-Aldrich SyndromeNo drug interventionstreatment3active_not_recruiting
NCT03399461
Targeted Literature Review and Subject Interviews in Wiskott-Aldrich Syndrome (WAS)No drug interventionsNot AvailableNot Availablecompleted
NCT03513328
Conditioning Regimen for Allogeneic Hematopoietic Stem-Cell Transplantationtreatment1 / 2completed
NCT01852370
Sequential Cadaveric Lung and Bone Marrow Transplant for Immune Deficiency DiseasesNo drug interventionstreatment1 / 2enrolling_by_invitation
NCT00004341
Study of Genetic and Molecular Defects in Primary Immunodeficiency DisordersNo drug interventionsNot AvailableNot Availableunknown_status
NCT01953016
Participation in a Research Registry for Immune DisordersNo drug interventionsNot AvailableNot Availablecompleted
NCT00909363
Thrombocytopenia and Bleeding in Wiskott-Aldrich Syndrome (WAS) Patientstreatment2terminated
NCT00220766
Rapid Infusion of Immune Globulin Intravenous (Human) In Primary Immunodeficiency Patientstreatment3completed
NCT05687474
Baby Detect : Genomic Newborn ScreeningNo drug interventionsNot AvailableNot Availablerecruiting
NCT03198195
Post-transplant Cyclophosphamide in Wiskott-Aldrich SyndromeNo drug interventionsNot AvailableNot Availableunknown_status
NCT00160355
Haploidentical Hematopoietic Stem Cell Transplantation Patients With Wiskott-Aldrich Syndrometreatment1completed
NCT01917708
Bone Marrow Transplant With Abatacept for Non-Malignant Diseasessupportive_care1completed