Wolman's Disease
Also known as: Wolman Disease / Other lipid storage disorders / Wolman's disease (disorder) / Lysosomal acid lipase deficiency / Lysosomal acid lipase deficiency (disorder)
| Drug | Drug Name | Drug Description |
|---|
| Drug | Drug Name | Target | Type |
|---|
| Drug | Drug Name | Phase | Status | Count |
|---|---|---|---|---|
| DB01272 | Alglucosidase alfa | 1 | Recruiting | 1 |
| DB09051 | Elosulfase alfa | 1 | Recruiting | 1 |
| DB01279 | Galsulfase | 1 | Recruiting | 1 |
| DB01271 | Idursulfase | 1 | Recruiting | 1 |
| DB00090 | Laronidase | 1 | Recruiting | 1 |
| DB11563 | Sebelipase alfa | 1 | Recruiting | 1 |
| DB12366 | Vestronidase alfa | 1 | Recruiting | 1 |
| DB00087 | Alemtuzumab | 2 | Completed | 1 |
| DB00087 | Alemtuzumab | 2 | Terminated | 1 |
| DB01008 | Busulfan | 2 | Terminated | 1 |
| DB00631 | Clofarabine | 2 | Completed | 1 |
| DB06189 | Clofarabine | 2 | Completed | 1 |
| DB00531 | Cyclophosphamide | 2 | Terminated | 1 |
| DB01005 | Hydroxyurea | 2 | Completed | 1 |
| DB01042 | Melphalan | 2 | Completed | 1 |
| DB01008 | Busulfan | 2 / 3 | Completed | 1 |
| DB00531 | Cyclophosphamide | 2 / 3 | Completed | 1 |
| DB11563 | Sebelipase alfa | 2 / 3 | Completed | 1 |
| DB11563 | Sebelipase alfa | 2 / 3 | Terminated | 1 |