Wolman's Disease

Also known as: Wolman Disease / Disease, Wolman / Lipidoses NOS / Cerebrotendinous cholesterosis [van Bogaert-Scherer-Epstein]

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB01272Alglucosidase alfa1Not Yet Recruiting1
DB09051Elosulfase alfa1Not Yet Recruiting1
DB01279Galsulfase1Not Yet Recruiting1
DB01271Idursulfase1Not Yet Recruiting1
DB00090Laronidase1Not Yet Recruiting1
DB11563Sebelipase alfa1Not Yet Recruiting1
DB12366Vestronidase alfa1Not Yet Recruiting1
DB00087Alemtuzumab2Completed1
DB00087Alemtuzumab2Terminated1
DB01008Busulfan2Terminated1
DB00631Clofarabine2Completed1
DB06189Clofarabine2Completed1
DB00531Cyclophosphamide2Terminated1
DB01005Hydroxyurea2Completed1
DB01042Melphalan2Completed1
DB01008Busulfan2 / 3Completed1
DB00531Cyclophosphamide2 / 3Completed1
DB11563Sebelipase alfa2 / 3Completed1
DB11563Sebelipase alfa2 / 3Terminated1