Pyruvate kinase deficiency anaemia

Also known as: Pyruvate Kinase Deficiency Anemia / Anemia due to pyruvate kinase deficiency / HNSHA due to pyruvate kinase deficiency (disorder)

DrugDrug NameDrug Description
DB16236MitapivatA pyruvate kinase activator used to treat hemolytic anemia in adults with pyruvate kinase (PK) deficiency.
DrugDrug NamePhaseStatusCount