Other Miscellaneous Therapeutic Agents
- Other Miscellaneous Therapeutic Agents
- Accession Number
Drug Drug Description Botulinum toxin type B A purified form of botulinum toxin type B used to block acetylcholine release in the treatment of cervical dystonia and sialorrhea. Botulinum toxin type A A purified form of botulinum toxin type A used to block acetylcholine release in the treatment of chronic sialorrhea, muscle spasticity, and dystonia, as well as in cosmetic applications. Nitisinone A hydroxyphenylpyruvate dioxygenase inhibitor used as an adjunct to dietary restrictions for the treatment of hereditary tyrosinemia type 1 (HT-1), which causes intolerance to tyrosine containing foods. Sapropterin A cofactor used as an adjunct to phenylalanine restriction in the treatment of phenylketonuria (PKU). Cysteamine A cystine depleting agent used to treat the effects of cystinosis. Cinacalcet A calcium sensing receptor agonist used to treat secondary hyperparathyroidism in chronic kidney disease and hypercalcemia in parathyroid carcinoma. Yohimbine An alpha-2-adrenergic blocker and sympatholytic found in supplements used to. Deoxycholic acid A cytolytic agent injected subcutaneously to improve the appearance submental fat. Cyproterone acetate A steroid used in combination with ethinyl estradiol to treat women with severe acne and symptoms of androgenization. Also used alone at much higher doses for palliative treatment of patients with prostate cancer Migalastat An alpha-galactosidase A chaperone used for the treatment of Fabry disease in patients with an amenable galactosidase alpha gene (GLA) variant. Dalfampridine A potassium channel blocker used for the improvement of motor function in patients with multiple sclerosis (MS). Betaine A methyl group donor used for the treatment of homocystinuria to decrease elevated homocysteine blood levels. Lanreotide A somatostatin analog used for the treatment of unresectable, well- or moderately-differentiated, locally advanced or metastatic gastroenteropancreatic neuroendocrine tumors and acromegaly. Eliglustat A glucosylceramide synthase used to treat type 1 Gaucher disease in patients who are CYP2D6 extensive, intermediate, or poor metabolizers, based on the FDA-approved test. Cobicistat A CYP3A inhibitor used to increase the systemic exposure of atazanavir or darunavir in combination with other antiretroviral agents in the treatment of HIV-1 infection. Oxygen An essential element for human survival used in clinical conditions in which there is a lack of oxygen, such as, but not limited to, anoxia, hypoxia or dyspnea. Water A naturally-occurring element used as an ingredient and vehicle in various pharmaceutical preparations of water. Nitrogen A cryogenic agent used to treat various benign and malignant skin lesions. Sodium chloride An ingredient found in a variety of nutritional products as a source of electrolytes and water. Helium A gas used for medical conditions where there is a need for increased oxygen intake, such as upper airway obstruction in asthma and COPD. Carbon dioxide A naturally-occurring gas used as a insufflation gas during minimally invasive surgeries to enlarge and stabilize body cavities to provide better visibility of the surgical area. Medical air A mixture of gases that is primarily composed of nitrogen and oxygen used for respiratory support in a variety of conditions. Patisiran A transthyretin-directed small interfering RNA used to treat polyneuropathy of hereditary transthyretin-mediated amyloidosis. Miglustat A glucosylceramide synthase inhibitor used for the management of mild to moderate type I Gaucher disease for patients who are not candidates for whole enzyme replacement. Givosiran A 5-aminolevulinic acid synthase-directed small interfering RNA (siRNA) used in the prophylaxis of acute hepatic porphyria. Risdiplam An oral mRNA splicing modifier used in the treatment of spinal muscular atrophy (SMA).
- Drugs & Drug Targets