Alpha-1 Anti-trypsin Deficiency

DBCOND0066043Congenital, Hereditary, and Neonatal Diseases and AbnormalitiesNutritional and Metabolic Diseases

Alpha-1 Anti-trypsin Deficiency is the indication for 1 drug in DrugBank. It is covered by 1 curated, structured indication.

Also known as
Alpha 1-Antitrypsin Deficiency · Alpha-1 Antitrypsin Deficiency · Alpha 1-Antitrypsin (AAT) Deficiency · Alpha 1 Antitrypsin Deficiency · Alpha 1-antitrypsin Deficiency (AATD)
Classified under
Indicated drugs

Resolves to

Vocabularies
MeSHM0029552ICD-10E88.01SNOMED CT154771007MedDRA10001806UMLSC0221757

What you can answer from here — as of October 26, 2026

1Indicated drugWith each drug's targets and mechanism
Listed above
1Structured indicationPopulation, line of therapy, route and combination as fields, not prose
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95Clinical trialsPhase, status and sponsor resolved per trial
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Which approved drugs for Alpha-1 Anti-trypsin Deficiency share a target, and which companies have late-stage candidates against it?

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