NCT02179333
| Preliminary Study of the Scale To Assess Ataxia and Neurologic Dysfunction (STAND) | No drug interventions | Not Available | Not Available | completed |
NCT01303406
| Patient Reported Outcomes in Friedreich's Ataxia Patients After Withdrawal From Treatment With Idebenone (PROTI) | | treatment | 3 | completed |
NCT02497534
| Biomarkers in Friedreich's Ataxia | No drug interventions | Not Available | Not Available | recruiting |
NCT01962363
| EPI-743 in Friedreich's Ataxia Point Mutations | | treatment | 2 | completed |
NCT01016366
| Safety Study of Carbamylated Erythropoietin to Treat Patients With the Neurodegenerative Disorder Friedreich's Ataxia | No drug interventions | treatment | 2 | completed |
NCT00697073
| Study to Assess the Safety and Tolerability of Idebenone in the Treatment of Friedreich's Ataxia Patients | | treatment | 3 | completed |
NCT02415127
| Safety, Tolerability and Efficacy of ACTIMMUNE® Dose Escalation in Friedreich's Ataxia | | treatment | 3 | completed |
NCT00993967
| Long-Term Safety and Tolerability of Idebenone in Friedreich's Ataxia Patients (MICONOS Extension) | | treatment | 3 | completed |
NCT01921868
| An Open-label Study of the Effects of Acetyl-L-Carnitine on Cardiovascular Outcomes in Friedreich's Ataxia | | treatment | Not Available | unknown_status |
NCT00803868
| Pilot Study of Varenicline (Chantix®) in the Treatment of Friedreich's Ataxia | | treatment | 2 / 3 | terminated |
NCT02840669
| A Study to Characterize the Cardiac Phenotype of Individuals With Friedreich's Ataxia (CARFA Study) | No drug interventions | diagnostic | Not Available | completed |
NCT02660112
| (+) Epicatechin to Treat Friedreich's Ataxia | | treatment | 2 | completed |
NCT00811681
| Effect of Pioglitazone Administered to Patients With Friedreich's Ataxia: Proof of Concept | | treatment | 3 | completed |
NCT02316314
| Characterization of the Cardiac Phenotype of Friedreich's Ataxia (FRDA) | No drug interventions | Not Available | Not Available | recruiting |
NCT01728064
| Safety and Efficacy of EPI-743 in Patients With Friedreich's Ataxia | | treatment | 2 | completed |
NCT00897221
| A Study Investigating the Long-term Safety and Efficacy of Deferiprone in Patients With Friedreich's Ataxia | | treatment | 2 | completed |
NCT00631202
| Efficacy of Epoetin Alfa in Patients With Friedreich's Ataxia | | treatment | 2 | completed |
NCT01898884
| Safety and Pharmacology Study of VP 20629 in Adults With Friedreich's Ataxia | | treatment | 1 | completed |
NCT01035671
| Safety and Efficacy Study of A0001 in Subjects With Friedreich's Ataxia | | treatment | 2 | completed |
NCT02069509
| Patient Registry of the European Friedreich's Ataxia Consortium for Translational Studies (EFACTS) | No drug interventions | Not Available | Not Available | recruiting |
NCT02593773
| Safety, Tolerability and Efficacy of ACTIMMUNE® Dose Escalation in Friedreich's Ataxia Study | | treatment | 3 | completed |
NCT00530127
| A Study Investigating the Safety and Tolerability of Deferiprone in Patients With Friedreich's Ataxia | | treatment | 1 / 2 | completed |
NCT02445794
| A First in Human Study of RT001 in Patients With Friedreich's Ataxia | No drug interventions | treatment | 1 / 2 | completed |
NCT02797080
| Long-Term Safety Extension Study of ACTIMMUNE® (Interferon γ-1b) in Children and Young Adults With Friedreich's Ataxia | | treatment | 3 | completed |
NCT00537680
| Study to Assess the Efficacy, Safety and Tolerability of Idebenone in the Treatment of Friedreich's Ataxia | | treatment | 3 | completed |
NCT04102501
| A Study to Assess Efficacy, Long Term Safety and Tolerability of RT001 in Subjects With Friedreich's Ataxia | No drug interventions | treatment | 3 | completed |
NCT00905268
| A Study of Efficacy, Safety and Tolerability of Idebenone in the Treatment of Friedreich's Ataxia (FRDA) Patients | | treatment | 3 | completed |
NCT05485987
| A Study of Vatiquinone for the Treatment of Participants With Friedreich Ataxia | | treatment | 2 | active_not_recruiting |
NCT06496451
| Frataxin mRNA in Biofluids | No drug interventions | Not Available | Not Available | not_yet_recruiting |
NCT04268147
| Instrumented Data Exchange for Ataxia Study | No drug interventions | Not Available | Not Available | completed |
NCT03761511
| Study of the Efficacy and Safety of Nicotinamide in Patients With Friedreich Ataxia | | treatment | 2 | withdrawn |
NCT06054893
| A Study of Omaveloxolone in Children With Friedreich's Ataxia | | treatment | 1 | recruiting |
NCT03214588
| Efficacy, Tolerability, and Pharmacokinetics of Multiple Doses of Oral TAK-831 in Adults With Friedreich Ataxia | | treatment | 2 | completed |
NCT05874388
| Characterisation of the Cognitive Profile of Patients Suffering From Friedreich's Ataxia | No drug interventions | health_services_research | Not Available | not_yet_recruiting |
NCT00229632
| Idebenone to Treat Friedreich's Ataxia | | treatment | 2 | completed |
NCT04577352
| A Study to Assess the Efficacy and Safety of Vatiquinone for the Treatment of Participants With Friedreich Ataxia | | treatment | 2 / 3 | completed |
NCT05515536
| A Study to Assess the Safety and Efficacy of Vatiquinone in Participants With Friedreich Ataxia | | treatment | 3 | enrolling_by_invitation |
NCT03120013
| Rehabilitative Trial With Cerebello-Spinal tDCS in Neurodegenerative Ataxia | No drug interventions | treatment | Not Available | completed |
NCT02594917
| Genetic and Environmental Determinants That Control Metabolism in Pulmonary Hypertension | No drug interventions | Not Available | Not Available | completed |
NCT02424435
| Methylprednisolone Treatment of Friedreich Ataxia | | treatment | 0 | completed |
NCT00056186
| Transitional Life Events in Patients With Friedreich's Ataxia: Implications for Genetic Counseling | No drug interventions | Not Available | Not Available | completed |
NCT04649866
| Coronary Artery Disease in Patients With Friedreich's Ataxia | No drug interventions | diagnostic | Not Available | completed |
NCT04273165
| Safety and Efficacy of Etravirine in Friedreich Ataxia Patients | | treatment | 2 | completed |
NCT02035020
| A Phase IIa Trial to Test Safety and Efficacy Interferon Gamma Treatment in Elevating Frataxin Levels in FRDA Patients | No drug interventions | treatment | 2 | completed |
NCT04176991
| Single Ascending Dose Study of CTI-1601 Versus Placebo in Subjects With Friedreich's Ataxia | | treatment | 1 | completed |
NCT05285540
| Study to Evaluate DT-216 in Adult Patients With Friedreich Ataxia | No drug interventions | treatment | 1 | completed |
NCT04519567
| Multiple Ascending Dose Study of CTI-1601 Versus Placebo in Subjects With Friedreich's Ataxia | | treatment | 1 | completed |
NCT06016946
| Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study | No drug interventions | Not Available | Not Available | recruiting |
NCT00078481
| Phase 1 Trial of Idebenone to Treat Patients With Friedreich's Ataxia | | treatment | 1 | completed |
NCT05445323
| Gene Therapy for Cardiomyopathy Associated With Friedreich's Ataxia | No drug interventions | treatment | 1 / 2 | recruiting |
NCT00015808
| Safety Study of Idebenone to Treat Friedreich's Ataxia | | treatment | 1 | completed |
NCT04801303
| Evaluation of the Effects of Calcitriol's in the Neurological Symptoms of Friedreich's Ataxia Patients | | treatment | 4 | completed |
NCT05028764
| Determine Range of Tissue Frataxin Concentrations and Other Potential Biomarkers | No drug interventions | Not Available | Not Available | completed |
NCT01776164
| Early and Longitudinal Assessment of Neurodegeneration in the Brain and Spinal Cord in Friedreich's Ataxia | No drug interventions | Not Available | Not Available | completed |
NCT03888664
| Open Trail of γIFN for Friedreich Ataxia | No drug interventions | treatment | 2 | completed |
NCT01716221
| An Objective Double-blind Evaluation of Bupropion and Citalopram in an Individual With Friedreich Ataxia | | supportive_care | 4 | completed |
NCT06483802
| A Study of ASP2016 in Adults Who Have Heart Disease Associated With Friedreich Ataxia | | treatment | 1 | not_yet_recruiting |
NCT05943002
| Patient-reported, Health Economic and Psychosocial Outcomes in Friedreich Ataxia | No drug interventions | Not Available | Not Available | recruiting |
NCT01339884
| A Study of Resveratrol as Treatment for Friedreich Ataxia | | treatment | 1 / 2 | completed |
NCT02705547
| Rosuvastatin (Crestor) in Friedreich Ataxia | | treatment | 0 | completed |
NCT05573698
| Study to Evaluate Multiple Ascending Dose and Multi-Dose of DT-216 in Adult Patients With Friedreich Ataxia | No drug interventions | treatment | 1 | completed |
NCT06539598
| Respiratory Training in Friedreich's Ataxia | No drug interventions | other | Not Available | not_yet_recruiting |
NCT04817111
| NAD+ Precursor Supplementation in Friedreich's Ataxia | No drug interventions | other | 2 | completed |
NCT05302271
| Phase IA Study of AAVrh.10hFXN Gene Therapy for the Cardiomyopathy of Friedreich's Ataxia | | treatment | 1 | recruiting |
NCT04631224
| Longitudinal Analysis of Oral Communication in Friedreich's Ataxia | No drug interventions | Not Available | Not Available | completed |
NCT02255435
| RTA 408 Capsules in Patients With Friedreich's Ataxia - MOXIe | | treatment | 2 | active_not_recruiting |
NCT03933163
| Micronised Resveratrol as a Treatment for Friedreich Ataxia | | treatment | 2 | completed |
NCT03122925
| TCA Cycle in the Dentate in Friedreich's Ataxia | No drug interventions | Not Available | Not Available | completed |
NCT03917225
| A Clinical Study to Evaluate the Effect of MIN-102 on the Progression of Friedreich's Ataxia in Male and Female Patients | | treatment | 2 | completed |
NCT06447025
| An Open Label Extension Study of CTI-1601 in Subjects With Friedreich's Ataxia | | treatment | 2 | enrolling_by_invitation |
NCT04921930
| Evaluation of the Effect of Artesunate in Friedreich Ataxia (FA) | | treatment | 1 / 2 | completed |
NCT05168774
| FRDA Investigator Initiated Study (IIS) With Elamipretide | | treatment | 1 / 2 | completed |
NCT01493973
| Efficacy Study of Epoetin Alfa in Friedreich Ataxia | | treatment | 2 | completed |
NCT01965327
| Interferon Gamma-1b in Friedreich Ataxia (FRDA) | | treatment | 2 | completed |
NCT05579691
| A Double-Blind, Placebo-Controlled, Dose Exploration Study of CTI-1601 in Adult Subjects With Friedreich's Ataxia | | treatment | 2 | completed |
NCT04255680
| A Study to Assess Variation in Potential Biomarkers in Friedreich Ataxia | No drug interventions | Not Available | Not Available | completed |
NCT03090789
| FA Clinical Outcome Measures | No drug interventions | Not Available | Not Available | recruiting |
NCT03418740
| Neurology Measures in FA Children | No drug interventions | Not Available | Not Available | completed |
NCT00224640
| Iron-Chelating Therapy and Friedreich Ataxia | | treatment | 1 / 2 | completed |
NCT01793168
| Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford | No drug interventions | Not Available | Not Available | recruiting |
NCT06560346
| Understanding the Natural History Early in the Course or Presentation of Friedreich Ataxia | No drug interventions | Not Available | Not Available | not_yet_recruiting |
NCT00824512
| Efficacy of EGb761 in Patients Suffering From Friedreich Ataxia | | supportive_care | 2 | completed |
NCT04564495
| Home Based Tele-exercise for People With Chronic Neurological Impairments | No drug interventions | treatment | Not Available | active_not_recruiting |
NCT04349514
| A Natural History Study to TRACK Brain and Spinal Cord Changes in Individuals With Friedreich Ataxia (TRACK-FA) | No drug interventions | Not Available | Not Available | active_not_recruiting |
NCT04346238
| Characterization of the Interruptions of the GAA Expansion and Study of Their Influence on the Severity of Friedreich's Ataxia | No drug interventions | Not Available | Not Available | unknown_status |