Duchenne Muscular Dystrophy
Also known as: Muscular Dystrophy, Duchenne Type / DMD / Muscular Dystrophy / Muscular Dystrophies / Muscular Dystrophy (DMD) / Duchenne Muscular Distrophy (DMD) / Dystrophy, Muscular / Duchenne's Muscular Dystrophy / Duchenne Muscular Dystrophy (DMD) / Duchenne Dystrophy Muscular / Duchenne's Muscular Dystrophy (DMD) / Muscular Dystrophy, Duchenne / Muscular dystrophy NOS / Muscular dystrophy (disorder) / Becker muscular dystrophy (disorder) / Duchenne muscular dystrophy (disorder)
| Drug | Drug Name | Drug Description |
|---|---|---|
| DB05016 | Ataluren | A medication used for the treatment of Duchenne muscular dystrophy. |
| DB14984 | Casimersen | An antisense phosphorodiamidate morpholino oligonucleotide used to treat Duchenne muscular dystrophy patients with mutations amenable to exon 45 skipping. |
| DB11921 | Deflazacort | A corticosteroid used to treat Duchenne muscular dystrophy. |
| DB16802 | Delandistrogene moxeparvovec | A gene therapy used to treat Duchenne Muscular Dystrophy in ambulatory children with DMD gene mutation. |
| DB06014 | Eteplirsen | An antisense oligonucleotide used to treat Duchenne muscular dystrophy (DMD) in patients with a confirmed mutation of the DMD gene that is amenable to exon 51 skipping. |
| DB12645 | Givinostat | A histone deacetylase inhibitor indicated for the treatment of Duchenne Muscular Dystrophy (DMD). |
| DB15593 | Golodirsen | A drug used to treat certain mutations that cause Duchenne muscular dystrophy (DMD). |
| DB15114 | Vamorolone | A synthetic glucocorticoid used as an anti-inflammatory and immunosuppressant in the management of Duchenne muscular dystrophy (DMD). |
| DB15005 | Viltolarsen | An antisense phosphorodiamidate morpholino oligonucleotide specific for exon 53 of the human DMD gene that is capable of inducing exon 53 skipping to produce a functional truncated dystrophin protein in Duchenne muscular dystrophy patients with specific underlying mutations. |