Duchenne Muscular Dystrophy (DMD)

Also known as: Muscular Dystrophy, Duchenne Type / DMD / Muscular Dystrophy / Muscular Dystrophies / Muscular Dystrophy (DMD) / Duchenne Muscular Distrophy (DMD) / Dystrophy, Muscular / Duchenne's Muscular Dystrophy / Duchenne Dystrophy Muscular / Duchenne Muscular Dystrophy / Duchenne's Muscular Dystrophy (DMD) / Muscular Dystrophy, Duchenne / Muscular dystrophy NOS / Muscular dystrophy (disorder) / Becker muscular dystrophy (disorder) / Duchenne muscular dystrophy (disorder)

DrugDrug NameDrug Description
DB05016AtalurenA medication used for the treatment of Duchenne muscular dystrophy.
DB14984CasimersenAn antisense phosphorodiamidate morpholino oligonucleotide used to treat Duchenne muscular dystrophy patients with mutations amenable to exon 45 skipping.
DB11921DeflazacortA corticosteroid used to treat Duchenne muscular dystrophy.
DB16802Delandistrogene moxeparvovecA gene therapy used to treat Duchenne Muscular Dystrophy in ambulatory children with DMD gene mutation.
DB06014EteplirsenAn antisense oligonucleotide used to treat Duchenne muscular dystrophy (DMD) in patients with a confirmed mutation of the DMD gene that is amenable to exon 51 skipping.
DB12645GivinostatA histone deacetylase inhibitor indicated for the treatment of Duchenne Muscular Dystrophy (DMD).
DB15593GolodirsenA drug used to treat certain mutations that cause Duchenne muscular dystrophy (DMD).
DB15114VamoroloneA synthetic glucocorticoid used as an anti-inflammatory and immunosuppressant in the management of Duchenne muscular dystrophy (DMD).
DB15005ViltolarsenAn antisense phosphorodiamidate morpholino oligonucleotide specific for exon 53 of the human DMD gene that is capable of inducing exon 53 skipping to produce a functional truncated dystrophin protein in Duchenne muscular dystrophy patients with specific underlying mutations.
DrugDrug NamePhaseStatusCount
DB00203Sildenafil0Completed1
DB00820Tadalafil0Completed1
DB00820Tadalafil0Terminated1
DB18367Allogeneic umbilical cord mesenchymal stem cells1Completed1
DB00125Arginine1Completed2
DB16992BLS-M221Completed1
DB16906Bocidelpar1Terminated1
DB14984Casimersen1Completed1
DB11921Deflazacort1Completed2
DB16802Delandistrogene moxeparvovec1Active Not Recruiting1
DB13688Drisapersen1Completed1
DB12888Ezutromid1Completed2
DB00798Gentamicin1Completed2
DB01050Ibuprofen1Completed1
DB15258Imlifidase1Active Not Recruiting1
DB00883Isosorbide dinitrate1Completed1
DB00331Metformin1Completed1
DB00860Prednisolone1Terminated1
DB12861Rimeporide1Completed1
DB18983Sevasemten1Completed2
DB00203Sildenafil1Completed1
DB00421Spironolactone1Terminated1
DB17940Suvodirsen1Completed1
DB00820Tadalafil1Completed1
DB00675Tamoxifen1Completed1
DB16993Vesleteplirsen1Completed1
DB15005Viltolarsen1Completed1
DB17855AAV1-FS3441 / 2Completed1
DB18621AOC-10201 / 2Recruiting1
DB15744Allogeneic Cardiosphere-Derived Cells1 / 2Completed1
DB17003BMN-0441 / 2Completed1
DB17004BMN-0451 / 2Terminated1
DB17008BMN-0531 / 2Terminated1
DB06168Canakinumab1 / 2Active Not Recruiting1
DB18130DYNE-2511 / 2Recruiting1
DB19253Dexepicatechin1 / 2Completed1
DB15010Edasalonexent1 / 2Completed1
DB06014Eteplirsen1 / 2Completed2
DB12645Givinostat1 / 2Completed1
DB15593Golodirsen1 / 2Completed1
DB04866Halofuginone1 / 2Terminated1
DB15726Human Umbilical Cord Mesenchymal Stem Cells1 / 2Not Yet Recruiting1
DB15726Human Umbilical Cord Mesenchymal Stem Cells1 / 2Unknown Status1
DB01277Mecasermin1 / 2Completed1
DB00806Pentoxifylline1 / 2Completed2
DB19132Renadirsen1 / 2Completed1
DB16337Talditercept alfa1 / 2Terminated1
DB16993Vesleteplirsen1 / 2Terminated1
DB17848WVE-N5311 / 2Active Not Recruiting1
DB17901rAAVrh74.MCK.GALGT21 / 2Active Not Recruiting1
DB17901rAAVrh74.MCK.GALGT21 / 2Withdrawn1
DB18582scAAV9.U7.ACCA1 / 2Active Not Recruiting1
DB18620AOC 10012Active Not Recruiting1
DB04997ATL11022Active Not Recruiting1
DB15744Allogeneic Cardiosphere-Derived Cells2Active Not Recruiting1
DB15744Allogeneic Cardiosphere-Derived Cells2Completed2
DB06696Arbekacin2Unknown Status1
DB05016Ataluren2Completed5
DB05016Ataluren2Terminated3
DB17003BMN-0442Terminated2
DB18884Brogidirsen2Recruiting1
DB14984Casimersen2Completed1
DB15083Domagrozumab2Terminated2
DB13688Drisapersen2Completed2
DB13688Drisapersen2Terminated1
DB06014Eteplirsen2Completed6
DB06014Eteplirsen2Terminated1
DB12888Ezutromid2Terminated1
DB15593Golodirsen2Completed1
DB04866Halofuginone2Terminated2
DB09081Idebenone2Completed2
DB00130L-Glutamine2Completed1
DB12877Oxatomide2Completed1
DB14952Pamrevlumab2Terminated1
DB00860Prednisolone2Completed1
DB00635Prednisone2Completed1
DB00635Prednisone2Recruiting1
DB00635Prednisone2Withdrawn1
DB15116Ramatercept2Terminated2
DB19132Renadirsen2Active Not Recruiting1
DB15762Satralizumab2Not Yet Recruiting1
DB18983Sevasemten2Recruiting2
DB00203Sildenafil2Terminated1
DB00820Tadalafil2Not Yet Recruiting1
DB01284Tetracosactide2Terminated1
DB09270Ubidecarenone2Completed1
DB15114Vamorolone2Active Not Recruiting1
DB15114Vamorolone2Completed4
DB16993Vesleteplirsen2Active Not Recruiting1
DB15005Viltolarsen2Completed3
DB00612Bisoprolol2 / 3Recruiting1
DB12116Epigallocatechin gallate2 / 3Completed1
DB12645Givinostat2 / 3Enrolling by Invitation1
DB00130L-Glutamine2 / 3Completed1
DB00722Lisinopril2 / 3Completed1
DB17940Suvodirsen2 / 3Terminated1
DB00820Tadalafil2 / 3Recruiting1
DB16337Talditercept alfa2 / 3Completed1
DB09270Ubidecarenone2 / 3Completed1
DB15744Allogeneic Cardiosphere-Derived Cells3Recruiting1
DB05016Ataluren3Completed3
DB05016Ataluren3Enrolling by Invitation1
DB05016Ataluren3Terminated1
DB14984Casimersen3Active Not Recruiting1
DB14984Casimersen3Terminated1
DB00155Citrulline3Completed1
DB11921Deflazacort3Completed1
DB11921Deflazacort3Withdrawn1
DB13688Drisapersen3Completed1
DB13688Drisapersen3Terminated2
DB13688Drisapersen3Withdrawn1
DB15010Edasalonexent3Completed1
DB15010Edasalonexent3Terminated1
DB00584Enalapril3Completed1
DB00700Eplerenone3Completed1
DB06014Eteplirsen3Active Not Recruiting1
DB06014Eteplirsen3Completed1
DB16800Fordadistrogene movaparvovec3Recruiting1
DB12645Givinostat3Completed1
DB12645Givinostat3Recruiting1
DB15593Golodirsen3Active Not Recruiting1
DB15593Golodirsen3Terminated1
DB09081Idebenone3Completed1
DB09081Idebenone3Terminated2
DB00130L-Glutamine3Completed1
DB00331Metformin3Completed1
DB00264Metoprolol3Recruiting1
DB04861Nebivolol3Completed1
DB14952Pamrevlumab3Terminated2
DB00635Prednisone3Completed3
DB00635Prednisone3Terminated1
DB00421Spironolactone3Completed1
DB00820Tadalafil3Terminated1
DB00675Tamoxifen3Completed1
DB15005Viltolarsen3Active Not Recruiting1
DB15005Viltolarsen3Completed1
DB00630Alendronic acid4Completed1
DB01136Carvedilol4Unknown Status2
DB15593Golodirsen4Terminated1
DB10791Influenza A virus A/California/7/2009 X-179A (H1N1) antigen (formaldehyde inactivated)4Completed1
DB14445Influenza A virus A/Victoria/210/2009 X-187 (H3N2) antigen (formaldehyde inactivated)4Completed1
DB10794Influenza B virus B/Brisbane/60/2008 antigen (formaldehyde inactivated)4Completed1
DB00860Prednisolone4Recruiting1
DB00178Ramipril4Unknown Status1
DB00884Risedronic acid4Completed1
DB15005Viltolarsen4Active Not Recruiting1
DB01001AlbuterolNot AvailableCompleted1
DB11921DeflazacortNot AvailableApproved for Marketing1
DB00633DexmedetomidineNot AvailableCompleted1
DB13688DrisapersenNot AvailableNo Longer Available1
DB00700EplerenoneNot AvailableCompleted1
DB09081IdebenoneNot AvailableNo Longer Available1
DB01221KetamineNot AvailableCompleted1
DB00722LisinoprilNot AvailableCompleted1
DB00678LosartanNot AvailableCompleted1
DB00621OxandroloneNot AvailableCompleted1
DB00624TestosteroneNot AvailableCompleted1
DB15114VamoroloneNot AvailableAvailable1
DB15005ViltolarsenNot AvailableApproved for Marketing1