NCT05688072
Trunk Oriented Exercises Versus Whole-body Vibration for Duchenne Muscular Dystrophy No drug interventions treatment Not Available completed NCT06244082
Ph2 Open-label Study of AOC 1044 in Duchenne Muscular Dystrophy Participants with Mutations Amenable to Exon44 Skipping No drug interventions treatment 2 recruiting NCT06581887
Defining Outcome Measures for Behavioural and Emotional Problems in Dystrophinopathies No drug interventions Not Available Not Available recruiting NCT03649919
Multi-center Clinical Study on the Diagnosis and Treatment Management of Rare Neurological Disease in Children No drug interventions Not Available Not Available withdrawn NCT05102916
Swiss Registry for Neuromuscular Disorders No drug interventions Not Available Not Available recruiting NCT01890616
Constipation and Gut Transit in DMD Patients No drug interventions Not Available Not Available completed NCT05635266
Tissue Repository Providing Annotated Biospecimens for Approved Investigator-directed Biomedical Research Initiatives No drug interventions Not Available Not Available recruiting NCT06290713
Vasodilator and Exercise Study for DMD (VASO-REx) treatment 2 recruiting NCT04337112
The Expanded Access Use of Viltolarsen in Duchenne Muscular Dystrophy With Confirmed Exon 53 Amenable Mutation Not Available Not Available approved_for_marketing NCT01961557
Evaluating a New Knee-Ankle-Foot Brace to Improve Gait in Children With Movement Disorders No drug interventions device_feasibility Not Available recruiting NCT05237973
Investigational Use of Neuromuscular Ultrasound No drug interventions Not Available Not Available recruiting NCT05726591
Evaluating Long-term Use of a Pediatric Robotic Exoskeleton (P.REX/Agilik) to Improve Gait in Children With Movement Disorders No drug interventions device_feasibility Not Available recruiting NCT00001164
Studies of Patients With Skin Disease, Patients With Neurological Degenerations, and Normal Volunteers No drug interventions Not Available Not Available completed NCT01459302
Genetic Study of Familial and Sporadic ALS/Motor Neuron Disease, Miyoshi Myopathy and Other Neuromuscular Disorders No drug interventions Not Available Not Available enrolling_by_invitation NCT00313677
Clinical Trial Readiness for the Dystroglycanopathies No drug interventions Not Available Not Available recruiting NCT04154098
Evaluation of a Textile Scapula Orthosis No drug interventions basic_science Not Available completed NCT01950897
Muscle Tissue Bank for Muscular Dystrophy No drug interventions Not Available Not Available completed NCT02241928
Stem Cell Therapy in Muscular Dystrophy No drug interventions treatment 1 withdrawn NCT01882400
Assessment of Response to Treatment of Osteoporosis With Oral Bisphosphonates in Patients With Muscular Dystrophy prevention 4 completed NCT01633242
Heart Imaging in Children With Muscular Dystrophy No drug interventions Not Available Not Available terminated NCT00912041
BrainGate2: Feasibility Study of an Intracortical Neural Interface System for Persons With Tetraplegia No drug interventions other Not Available recruiting NCT00518817
The Cardiovascular Genetic and Therapeutic Implications of Muscular Dystrophy No drug interventions Not Available Not Available unknown_status NCT00138931
Genetics of Cardiovascular and Neuromuscular Disease No drug interventions Not Available Not Available recruiting NCT01990976
Study of Morphology and Functional Magnetic Resonance Imaging (MRI) Muscle Patients With Muscular Dystrophy Type FSHD Benefiting a Physical Training Introduced. No drug interventions Not Available Not Available completed NCT01393444
ECoG Direct Brain Interface for Individuals With Upper Limb Paralysis No drug interventions Not Available Not Available completed NCT01834040
Study Safety and Efficacy of BMMNC for the Patient With Duchenne Muscular Dystrophy No drug interventions treatment 1 / 2 unknown_status NCT04035967
Investigation of Parents' Anxiety Level and Health Related Quality of Life in Different Types of Physical Disabilities No drug interventions Not Available Not Available completed NCT01451281
Studying Skeletal Muscle, Heart, and Diaphragm Imaging in Boys With Duchenne Muscular Dystrophy No drug interventions Not Available Not Available completed NCT00082108
Myotonic Dystrophy and Facioscapulohumeral Muscular Dystrophy Registry No drug interventions Not Available Not Available recruiting NCT04038138
Clinical Trial Readiness Network FSHD France: Prospective 24 Months MRI Study No drug interventions other Not Available active_not_recruiting NCT02104921
Innovative Ultrasound Technology in Neuromuscular Disease No drug interventions Not Available Not Available completed NCT02653833
The Study of Skeletal Muscle Blood Flow in Becker Muscular Dystrophy basic_science 0 terminated NCT00622453
Arrhythmias in Myotonic Muscular Dystrophy No drug interventions Not Available Not Available completed NCT05228405
Awareness Levels of Caregivers of Disabled Children No drug interventions Not Available Not Available completed NCT04461561
Using NPT to Evaluate Providing PPC as ELNEC-PPC WBT for Nurses No drug interventions other Not Available unknown_status NCT03840928
PatientSpot Formerly Known as ArthritisPower No drug interventions Not Available Not Available recruiting NCT02218593
WREX Outcome Study No drug interventions Not Available Not Available completed NCT01790178
Ultrasound in Muscle Biopsy No drug interventions Not Available Not Available completed NCT02815878
Enhance Wellness for Individuals With Long-Term Physical Disabilities No drug interventions health_services_research Not Available completed NCT05470478
iBCI Optimization for Veterans With Paralysis No drug interventions other Not Available not_yet_recruiting NCT02522507
A Peer E-mentoring Intervention to Improve Employment No drug interventions treatment Not Available completed NCT05230459
A Study to Evaluate the Safety of AB-1003 (Previously LION-101) in Subjects With Genetic Confirmation of LGMD2I/R9 (Part1) No drug interventions treatment 1 / 2 recruiting NCT04574934
Effect of Aquatic Therapy on Pulmonary Functions in Patients With Muscular Dystrophy No drug interventions treatment Not Available unknown_status NCT02124616
National Registry for Egyptian Pediatric Neuromuscular Diseases No drug interventions Not Available Not Available unknown_status NCT05644522
Nomad P-KAFO Study No drug interventions treatment Not Available recruiting NCT05715957
Follow-up Study on Female Carriers With DMD Gene Variants No drug interventions Not Available Not Available not_yet_recruiting NCT06363526
Effectiveness of 5-week Digital Respiratory Practice in a Group of Children With Duchenne Muscular Dystrophy and Becker Muscular Dystrophy. No drug interventions treatment Not Available not_yet_recruiting NCT01834066
Study Safety and Efficacy of Bone Marrow Derived Autologous Cells for the Treatment of Muscular Dystrophy. No drug interventions treatment 1 / 2 unknown_status NCT02428673
Effects of Standing on Non-Ambulatory Children With Neuromuscular Conditions No drug interventions treatment Not Available completed NCT02532244
Genetics of Pediatric-Onset Motor Neuron and Neuromuscular Diseases No drug interventions Not Available Not Available recruiting NCT00004568
Study of Inherited Neurological Disorders No drug interventions Not Available Not Available recruiting NCT00866112
A Randomized Exercise Trial for Wheelchair Users No drug interventions Not Available Not Available completed NCT02745938
GDF-15 as a Biomarker for Mitochondrial Disease No drug interventions Not Available Not Available completed NCT05479981
Extension of AOC 1001-CS1 (MARINA) Study in Adult Myotonic Dystrophy Type 1 (DM1) Patients treatment 2 active_not_recruiting NCT03981289
Defining Clinical Endpoints in Limb Girdle Muscular Dystrophy (LGMD) No drug interventions Not Available Not Available active_not_recruiting NCT05257473
Defining Endpoints in Becker Muscular Dystrophy No drug interventions Not Available Not Available recruiting NCT02921321
Pilot Study of Cardiac MR in Patients With Muscular Dystrophy No drug interventions Not Available Not Available active_not_recruiting NCT05945784
Exploring Accessible Beauty for Individuals With Upper Extremity Deficits No drug interventions Not Available Not Available completed NCT01826487
Phase 3 Study of Ataluren in Participants With Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD) treatment 3 completed NCT04798378
NuroSleeve Powered Brace & Stimulation System to Restore Arm Function No drug interventions supportive_care Not Available recruiting NCT04694456
Pro-inflammatory Cytokines in Facioscapulohumeral Muscular Dystrophy (CYTOKINE-FSH) No drug interventions other Not Available completed NCT05730842
Absorption, Metabolism, Excretion and Absolute Bioavailability of EDG-5506 in Healthy Volunteers treatment 1 completed NCT04313049
LARA: Use of JACO2 Controlled by Joystick or by Voice Control System, in Muscular Dystrophy No drug interventions supportive_care Not Available completed NCT01910649
A Phase I/II, Open Label, Escalating Dose, Pilot Study to Assess Effect, Safety, Tolerability and PK of Multiple SC Doses of Drisapersen in Patients With Duchenne Muscular Dystrophy and to Assess the Potential for IV Dosing as an Alternative Route of Administration treatment 2 terminated NCT04392518
Telerehabilitation in Proximal Muscle Weakness No drug interventions treatment Not Available unknown_status NCT04468919
Optimizing BCI-FIT: Brain Computer Interface - Functional Implementation Toolkit No drug interventions basic_science Not Available recruiting NCT03127241
User-centred Assistive System for Arm Functions in Neuromuscular Subjects No drug interventions supportive_care Not Available completed NCT04045158
Diaphragm Ultrasound in Neuromuscular Disorders No drug interventions Not Available Not Available unknown_status NCT02895763
Quality of Life in Neuromuscular Disease No drug interventions Not Available Not Available completed NCT02109692
Evaluation of Muscle miRNA as Biomarkers in Dystrophinopathies No drug interventions health_services_research Not Available unknown_status NCT03951844
Wearability, Saefty and Usability Assessment for the Upper Limb Exoskeleton BRIDGE/EMPATIA No drug interventions other Not Available completed NCT05199246
Assessment of Safety and Acute Effects of a Lower-limb Powered Dermoskeleton in Patients With Neuromuscular Disorders No drug interventions other Not Available recruiting NCT01803412
A Study of the Safety, Tolerability & Efficacy of Long-term Administration of Drisapersen in US & Canadian Subjects treatment 3 terminated NCT04677010
Cycle Exercise in Wheelchair Users With Muscular Dystrophy or Cerebral Palsy No drug interventions treatment Not Available completed NCT04313595
Device for Breathing Frequency Monitoring in Muscular Dystrophy No drug interventions supportive_care Not Available completed NCT03490214
Non-invasive Imaging of Muscle Structure in Duchenne Muscular Dystrophy Using Multispectral Optoacoustic Tomography No drug interventions diagnostic Not Available completed NCT01128855
A Double-blind, Escalating Dose, Randomized, Placebo-controlled Study Assessing PK, Safety, Tolerability in Non-ambulant DMD Subjects treatment 1 completed NCT05035823
COMMAND Early Feasibility Study: Implantable BCI to Control a Digital Device for People With Paralysis No drug interventions device_feasibility Not Available active_not_recruiting NCT04009408
Expiratory Muscle Strength Training (EMST) in Neuromuscular Disorders No drug interventions treatment Not Available unknown_status NCT00674843
The Efficacy of Using Far Infrared Radiation to Manage Muscular Dystrophies No drug interventions treatment 1 unknown_status NCT06378203
Rehabilitation in Muscular Dystrophies From the Hospital Facility to the Home: Pilot Project [RIMUDI] No drug interventions treatment Not Available recruiting NCT05200702
Assessment of Safety and Acute Effects of a Knee-hip Powered Soft Exoskeleton in Patients With Neuromuscular Disorders No drug interventions other Not Available recruiting NCT05409079
Schulze Muscular Dystrophy Ability Clinical Study No drug interventions treatment Not Available recruiting NCT04308447
Ablelite Pediatric Device Clinical Study No drug interventions treatment Not Available unknown_status NCT01480245
Open Label Study of GSK2402968 in Subjects With Duchenne Muscular Dystrophy treatment 3 terminated NCT01890798
Drisapersen Duchenne Muscular Dystrophy (DMD) Treatment Protocol treatment 3 withdrawn NCT06094205
Feasibility of the BrainGate2 Neural Interface System in Persons With Tetraplegia (BG-Speech-02) No drug interventions other Not Available recruiting NCT03508583
Turkish Version of The Measure of Processes of Care (MPOC) No drug interventions Not Available Not Available unknown_status NCT03930628
Limb-Girdle Muscular Dystrophy Type 2I in Norway No drug interventions Not Available Not Available active_not_recruiting NCT03986671
Transmembrane Electromyography (TM-EMG) for the Assessment of Neuromuscular Function in the Oropharynx No drug interventions diagnostic Not Available completed NCT03317171
Safety and Efficacy of a Flavonoids- and omega3s-based Compound for the Treatment of Muscular Dystrophies No drug interventions treatment Not Available completed NCT03851107
The Effectiveness of Participation-focused Interventions on Body Functions of Youth With Physical Disabilities No drug interventions treatment Not Available completed NCT02432885
Myocardial Fibrosis Progression in Duchenne and Becker Muscular Dystrophy - ACE Inhibitor Therapy Trial treatment 3 completed NCT02685215
Prognostic Factors , Morbidity and Mortality in Patients With Neuromuscular Disorders Admitted in ICU No drug interventions Not Available Not Available unknown_status NCT06507215
Dysferlinopathy Protein in Peripheral Blood Monocytes. No drug interventions Not Available Not Available completed NCT01153932
Phase II Doubleblind Exploratory Study of GSK2402968 in Ambulant Subjects With Duchenne Muscular Dystrophy treatment 2 completed NCT02090959
An Extension Study of Ataluren (PTC124) in Participants With Nonsense Mutation Dystrophinopathy treatment 3 terminated NCT02641275
Self-management Training for Parents With Chronic Muscular Dystrophia No drug interventions supportive_care Not Available withdrawn NCT04525742
COVID-19 Pandemic and Parents of Disabled Children No drug interventions screening Not Available completed NCT03698149
ECoG BMI for Motor and Speech Control No drug interventions device_feasibility Not Available recruiting NCT01254019
A Clinical Study to Assess the Efficacy and Safety of GSK2402968 in Subjects With Duchenne Muscular Dystrophy treatment 3 completed NCT05492734
A Study to Assess the Feasibility of Non-invasive Dried Blood Sampling treatment 1 completed NCT05747924
Phase 1/2 Study of AOC 1020 in Adults With Facioscapulohumeral Muscular Dystrophy (FSHD) treatment 1 / 2 recruiting NCT06547216
Phase 2 Open-label Extension Study of AOC 1020 in Adults With Facioscapulohumeral Muscular Dystrophy (FSHD) treatment 2 enrolling_by_invitation NCT05126758
A Study of CAP-1002 in Ambulatory and Non-Ambulatory Patients With Duchenne Muscular Dystrophy treatment 3 recruiting NCT01568658
Genetic and Physical Study of Childhood Nerve and Muscle Disorders No drug interventions Not Available Not Available recruiting NCT02315339
European Home Mechanical Ventilation Registry No drug interventions Not Available Not Available terminated NCT05881122
Anti-inflammatory Diet Consultation for Those With Neuromuscular Disability No drug interventions supportive_care Not Available completed NCT00873782
Safety Study of Transvenous Limb Perfusion in Human Muscular Dystrophy No drug interventions treatment 1 completed NCT04187482
Myotonic Dystrophy Type 1 Aerobic Exercise Study No drug interventions supportive_care Not Available completed NCT03179631
Long-Term Outcomes of Ataluren in Duchenne Muscular Dystrophy treatment 3 completed NCT05724173
Feasibility of the BrainGate2 Neural Interface System in Persons With Tetraplegia No drug interventions other Not Available recruiting NCT04202627
Biomarker Development in LGMD2i No drug interventions Not Available Not Available completed NCT04733976
Bullying in Youth With Muscular Dystrophy and Congenital Myopathies No drug interventions Not Available Not Available completed NCT03627494
First Time in Human (FTIH) Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of Single and Repeat Doses of GSK3439171A in Healthy Subjects and to Assess Food Effect No drug interventions treatment 1 completed NCT00027391
Study of Albuterol and Oxandrolone in Patients With Facioscapulohumeral Dystrophy (FSHD) treatment Not Available completed NCT05081791
Exercise Therapy for Patients With Muscle Dystrophies No drug interventions treatment Not Available recruiting NCT03406780
A Study of CAP-1002 in Ambulatory and Non-Ambulatory Patients With Duchenne Muscular Dystrophy treatment 2 completed NCT01462292
A Clinical Study to Assess Two Doses of GSK2402968 in Subjects With Duchenne Muscular Dystrophy (DMD) treatment 2 completed NCT03811301
[BrainConnexion] - Neurodevice Phase I Trial No drug interventions other Not Available active_not_recruiting NCT01800604
Power Over Pain (POP) Study No drug interventions treatment Not Available completed NCT00494195
Gene Transfer Therapy for Treating Children and Adults With Limb Girdle Muscular Dystrophy Type 2D (LGMD2D) No drug interventions treatment 1 completed NCT05041114
SWITCH II Early Feasibility Study: Implantable BCI to Control a Digital Device for People With Paralysis No drug interventions treatment Not Available withdrawn NCT02515669
Study of an Investigational Drug, RO7239361 (BMS-986089), in Ambulatory Boys With DMD basic_science 1 / 2 terminated NCT01823783
Endomysial Fibrosis, Muscular Inflammatory Response and Calcium Homeostasis Dysfunction in Duchenne Muscular Dystrophy No drug interventions basic_science Not Available unknown_status NCT03507530
Effects of Fear of Falling on Physical Performance and Quality of Life in Children With Duchenne Muscular Dystrophy No drug interventions Not Available Not Available unknown_status NCT00207857
Test-Retest Reliability of Pulmonary Function Tests in Patients With Duchenne's Muscular Dystrophy No drug interventions Not Available Not Available withdrawn NCT02235844
Allogeneic Human Umbilical Cord Mesenchymal Stem Cells for a Single Male Patient With Duchenne Muscular Dystrophy (DMD) No drug interventions treatment 1 completed NCT06641895
Evaluation of the Safety and Efficacy of BBM-D101 to Treat Patients With Duchenne Muscular Dystrophy No drug interventions treatment 0 recruiting NCT06643923
Effects of Lumbopelvic Stabilization-based Physiotherapy and Rehabilitation Training in Duchenne Muscular Dystrophy No drug interventions treatment Not Available not_yet_recruiting NCT05524883
Safety, Tolerability, Pharmacodynamic, Efficacy, and Pharmacokinetic Study of DYNE-251 in Participants With Duchenne Muscular Dystrophy Amenable to Exon 51 Skipping treatment 1 / 2 recruiting NCT00654784
Efficacy and Tolerability of Idebenone in Boys With Cardiac Dysfunction Associated With Duchenne Muscular Dystrophy treatment 2 completed NCT02420379
Safety Study of Eteplirsen to Treat Early Stage Duchenne Muscular Dystrophy treatment 2 completed NCT01540409
Efficacy, Safety, and Tolerability Rollover Study of Eteplirsen in Subjects With Duchenne Muscular Dystrophy treatment 2 completed NCT02814019
A Phase III Double-blind Study With Idebenone in Patients With Duchenne Muscular Dystrophy (DMD) Taking Glucocorticoid Steroids treatment 3 terminated NCT06392724
A Study to Evaluate the Safety and Tolerability of GEN6050X in Duchenne Muscular Dystrophy. No drug interventions treatment 0 recruiting NCT05135663
Extension Study of NS-089/NCNP-02 in DMD No drug interventions treatment 2 active_not_recruiting NCT01478022
To Compare the Pharmacokinetics Profiles of ISO 20, IBU 200 and IBU Plus ISO Combinations 200 + 20 treatment 1 completed NCT02614820
The Safety, Efficacy and Tolerability of Remote Ischemic Preconditioning as a Therapy to DMD No drug interventions treatment Not Available unknown_status NCT01982695
Cardiomyopathy in DMD: Lisinopril vs. Losartan treatment Not Available completed NCT05990608
Peabody Developmental Motor Scaling In Children With Period Duchenne Muscular Dystrophy No drug interventions Not Available Not Available completed NCT01380964
Research of Biomarkers in Duchenne Muscular Dystrophy Patients No drug interventions Not Available Not Available completed NCT05516745
E-monitoring of PULMonary Function in Patients With Duchenne Muscular Dystrophy at Home" No drug interventions supportive_care Not Available recruiting NCT02255552
Study of Eteplirsen in DMD Patients treatment 3 completed NCT02036463
A Trial of Chronotherapy of Corticosteroids in Duchenne Muscular Dystrophy supportive_care 2 withdrawn NCT04322357
Twice Weekly Steroids and Exercise as Therapy for DMD supportive_care 2 recruiting NCT04184882
A Study to Assess the Safety, Tolerability and Preliminary Efficacy of ASP0367 (MA-0211) in Pediatric Male Participants With Duchenne Muscular Dystrophy (DMD) treatment 1 terminated NCT01761292
A Study to Assess Safety/Tolerability, pk, Effects on Histology, Clinical Parameters of Givinostat in Children With DMD treatment 1 / 2 completed NCT04254172
A Low Interventional Study to Monitor Activity Using Wearable Sensors in Duchenne Muscular Dystrophy No drug interventions Not Available Not Available terminated NCT02472990
Biomechanical and Morphological Changes in Dystrophic Muscle No drug interventions other Not Available unknown_status NCT05185622
A Study to Assess Vamorolone in Boys Ages 2 to <4 Years and 7 to <18 Years With Duchenne Muscular Dystrophy (DMD) treatment 2 completed NCT05967351
A Long-term Follow-up Study of Participants Who Received Delandistrogene Moxeparvovec (SRP-9001) in a Previous Clinical Study No drug interventions other 3 enrolling_by_invitation NCT06138639
A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE) No drug interventions treatment 1 / 2 recruiting NCT06597656
A Gene Transfer Therapy to Evaluate the Safety and Efficacy of Delandistrogene Moxeparvovec (SRP-9001) Following Therapeutic Plasma Exchange (Plasmapheresis) in Participants With Duchenne Muscular Dystrophy (DMD) and Pre-existing Antibodies to AAVrh74 No drug interventions treatment 1 recruiting NCT01247207
Study of Ataluren in Previously Treated Participants With Nonsense Mutation Dystrophinopathy (nmDBMD) treatment 3 enrolling_by_invitation NCT06450639
An Open-label Study to Assess the Efficacy and Safety of Satralizumab in Duchenne Muscular Dystrophy treatment 2 recruiting NCT02500381
Study of SRP-4045 (Casimersen) and SRP-4053 (Golodirsen) in Participants With Duchenne Muscular Dystrophy (DMD) treatment 3 active_not_recruiting NCT04004065
Two-Part Study for Dose Determination of Vesleteplirsen (SRP-5051) (Part A), Then Dose Efficacy (Part B) in Participants With Duchenne Muscular Dystrophy Amenable to Exon 51-Skipping Treatment treatment 2 active_not_recruiting NCT06366815
phenotypeS in Non Ambulant Duchenne Muscular Dystrophy No drug interventions Not Available Not Available recruiting NCT06606340
A Long-term Observational Study Evaluating Eteplirsen, Golodirsen, or Casimersen in Routine Clinical Practice Not Available Not Available enrolling_by_invitation NCT05540860
A Study of EDG-5506 in Children with Duchenne Muscular Dystrophy (LYNX) treatment 2 recruiting NCT05670730
Study of AOC 1044 in Healthy Adult Volunteers and Participants with Duchenne Muscular Dystrophy (DMD) Mutations Amenable to Exon 44 Skipping No drug interventions treatment 1 / 2 active_not_recruiting NCT05881408
A Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of Delandistrogene Moxeparvovec (SRP-9001) in Non-Ambulatory and Ambulatory Participants With Duchenne Muscular Dystrophy (DMD) No drug interventions treatment 3 recruiting NCT05933057
Efficacy, Safety and Tolerability of Givinostat in Non-ambulant Patients With Duchenne Muscular Dystrophy treatment 3 recruiting NCT06093100
Wearable Technology to Evaluate Hyperglycemia and HRV in DMD - Longitudinal Aim No drug interventions Not Available Not Available recruiting NCT06100887
Phase 2 Study of EDG-5506 in Children and Adolescents with Duchenne Muscular Dystrophy Previously Treated with Gene Therapy (FOX) treatment 2 recruiting NCT06128564
A Gene Delivery Study to Evaluate the Safety and Expression of Delandistrogene Moxeparvovec in Participants Under the Age of Four With Duchenne Muscular Dystrophy (DMD) No drug interventions treatment 2 recruiting NCT06565208
First in Human SAD/MAD Safety and PK Study With Adult DMD Safety and PK Cohort No drug interventions treatment 0 recruiting NCT06109103
Telerehabilitation-based Motor Imagery Training in Children With Duchenne Muscular Dystrophy No drug interventions treatment Not Available not_yet_recruiting NCT03375164
A Gene Transfer Therapy Study to Evaluate the Safety of Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) No drug interventions treatment 1 / 2 completed NCT06304064
Halt cardiomyOPathy progrEssion in Duchenne (HOPE-OLE) treatment 2 completed NCT01523964
DART Electrical Impedance Myography (EIM) Trial in Duchenne Muscular Dystrophy (DMD) and Healthy Controls No drug interventions Not Available Not Available completed NCT01388764
Safety, Tolerability and Effects of L-Arginine in Boys With Dystrophinopathy on Corticosteroids Not Available 1 completed NCT02525302
HT-100 Long-term Study in DMD Patients Who Completed HALO-DMD-02 treatment 2 terminated NCT03057002
UTSW HP [13-C] Pyruvate Injection in HCM No drug interventions Not Available Not Available recruiting NCT03335384
Relationship Between PFTs and Pdi in DMD No drug interventions health_services_research Not Available withdrawn NCT00847379
Phase 2B Extension Study of Ataluren (PTC124) in Duchenne/Becker Muscular Dystrophy (DMD/BMD) treatment 2 terminated NCT02835079
Treatment Effect of Tamoxifen on Patients With DMD treatment 1 completed NCT05683379
AFFINITY BEYOND: Anti-AAV8 Antibody Assessment Study of Boys With DMD No drug interventions Not Available Not Available recruiting NCT00839033
Evaluation of a Mechanical Device During Acute Respiratory Failure in Patients With Neuromuscular Disorders No drug interventions treatment 3 terminated NCT00592553
Phase 2B Study of PTC124 (Ataluren) in Duchenne/Becker Muscular Dystrophy (DMD/BMD) treatment 2 completed NCT02760277
An Extension Study to Assess Vamorolone in Boys With Duchenne Muscular Dystrophy (DMD) treatment 2 completed NCT03508947
Safety and Tolerability of WVE-210201 in Patients With Duchenne Muscular Dystrophy treatment 1 completed NCT00819845
Ramipril Versus Carvedilol in Duchenne and Becker Patients prevention 4 unknown_status NCT03642145
A Study of Deflazacort (Emflaza®) in Participants With Duchenne Muscular Dystrophy (DMD) treatment 3 withdrawn NCT03002298
Virtual Reality in Individuals With Duchenne Muscular Dystrophy No drug interventions treatment Not Available completed NCT02530905
Dose-Titration and Open-label Extension Study of SRP-4045 in Advanced Stage Duchenne Muscular Dystrophy (DMD) Patients treatment 1 completed NCT05641805
Physical Activity Level and Cognitive Functions in Children With Duchenne Muscular Dystrophy No drug interventions Not Available Not Available recruiting NCT02571205
Testosterone Therapy for Pubertal Delay in Duchenne Muscular Dystrophy Not Available Not Available completed NCT01963897
Duchenne Muscular Dystrophy < 18y in Norway: Genotype/Phenotype, Growth, Puberty, Bone Health and Quality of Life. No drug interventions Not Available Not Available completed NCT01126697
Clinical Trial of Coenzyme Q10 and Lisinopril in Muscular Dystrophies treatment 2 / 3 completed NCT06274983
DMD- Interactive Virtual Reality Study No drug interventions supportive_care Not Available active_not_recruiting NCT02667483
Study of DS-5141b in Patients With Duchenne Muscular Dystrophy treatment 1 / 2 completed NCT05967793
Effect of Kinesiology Taping on Head and Trunk Control in Children With Duchenne Muscular Dystrophy No drug interventions supportive_care Not Available recruiting NCT02246478
A Study of TAS-205 for Duchenne Muscular Dystrophy No drug interventions treatment 1 completed NCT00264888
Safety and Efficacy Study of PTC124 in Duchenne Muscular Dystrophy treatment 2 completed NCT05849688
Bicycle Training on Ventilatory Functions in Duchenne Muscular Dystrophy No drug interventions treatment Not Available not_yet_recruiting NCT04529707
Sleep Intervention in Young Boys With Duchenne Muscular Dystrophy No drug interventions treatment Not Available recruiting NCT06280209
A Phase 1/2 Study to Assess the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of BMN 351 in Participants With Duchenne Muscular Dystrophy No drug interventions treatment 1 / 2 recruiting NCT01037309
Phase I/II Study of PRO044 in Duchenne Muscular Dystrophy (DMD) treatment 1 / 2 completed NCT04179409
A 48-Week, Open Label, Study to Evaluate the Efficacy and Safety of AMONDYS 45, EXONDYS 51, VYONDYS 53 in Subjects With DuchenneMuscular Dystrophy Carrying Eligible DMD Duplications. treatment 2 completed NCT05110885
Public AttitudesTowards SMA and DMD Awareness, Newborn and Carrier Screening and Physiotherapy Practices No drug interventions Not Available Not Available unknown_status NCT01981915
Optimum Insufflation Capacity in NMD No drug interventions diagnostic Not Available completed NCT00468832
Longitudinal Study of the Natural History of Duchenne Muscular Dystrophy (DMD) No drug interventions Not Available Not Available unknown_status NCT05029232
Comprehensive Study of Duchenne Muscular Dystrophy at Sohag University Hospital No drug interventions screening Not Available unknown_status NCT01422200
Flu Vaccine Study in Neuromuscular Patients 2011 prevention 4 completed NCT01957059
A Phase I/II Study of BMN053 in Subjects With Duchenne Muscular Dystrophy (DMD) No drug interventions treatment 1 / 2 terminated NCT00606775
The Preventive Efficacy of Carvedilol on Cardiac Dysfunction in Duchenne Muscular Dystrophy prevention 4 unknown_status NCT01999075
Stacking Exercises Aid the Decline in FVC and Sick Time No drug interventions treatment 4 completed NCT03951675
The Burden of Access in Duchenne Muscular Dystrophy in the US No drug interventions Not Available Not Available completed NCT03541070
The Effect of Kinesiology Taping on Balance in Duchenne Muscular Dystrophy No drug interventions supportive_care Not Available completed NCT04335942
Characterization of the Postural Habits of Wheelchair Users Analysis of the Acceptability of International Recommendations in the Prevention of Pressure Sores Risk by Using a Connected Textile Sensor No drug interventions prevention Not Available completed NCT06402942
Gamified Occupational Therapy for Adolescents With Duchenne Muscular Dystrophy No drug interventions supportive_care Not Available recruiting NCT05693142
AFFINITY DUCHENNE: RGX-202 Gene Therapy in Participants With Duchenne Muscular Dystrophy (DMD) No drug interventions treatment 1 / 2 recruiting NCT03532542
An Extension Study to Evaluate Casimersen or Golodirsen in Patients With Duchenne Muscular Dystrophy treatment 3 terminated NCT05549999
Cultural Adaptation, Validity, and Reliability of the Turkish Version of North Star Ambulatory Assessment No drug interventions Not Available Not Available completed NCT04060199
Study to Assess the Efficacy and Safety of Viltolarsen in Ambulant Boys With DMD (RACER53) treatment 3 completed NCT03038399
Long-term Extension Study to Assess Vamorolone in Boys With Duchenne Muscular Dystrophy (DMD) treatment 2 completed NCT05338099
Determine the Safety and Dose of EN001 in Patients With Duchenne Muscular Dystrophy(DMD) No drug interventions treatment 1 completed NCT06379906
Upper Extremity Muscle Strength, Balance and Functional Skills in DMD No drug interventions Not Available Not Available completed NCT06103006
Remote Physiotherapy to Protect Physical Health in Duchenne Muscular Dystrophy No drug interventions treatment Not Available completed NCT02310906
Phase I/II Study of SRP-4053 in DMD Patients treatment 1 / 2 completed NCT03534349
Lower Limb Flexibility in Duchenne Muscular Dystrophy: Effects on Functional Performance No drug interventions Not Available Not Available completed NCT06079736
A Study Of PGN-EDO51 In Participants With Duchenne Muscular Dystrophy Amenable To Exon 51-Skipping Treatment No drug interventions treatment 2 recruiting NCT03786913
Quantitative Muscle Ultrasound as a Marker of Progression in Children With Muscular Diseases No drug interventions Not Available Not Available completed NCT02907619
An Open-label Extension Study To Evaluate Safety Of PF-06252616 In Boys With Duchenne Muscular Dystrophy treatment 2 terminated NCT05982119
Assessments in Patients With Muscular Pathology and in Control Subjects : The ActiLiège Next Study No drug interventions basic_science Not Available recruiting NCT02592941
Deflazacort Expanded Access Program for Children, Adolescents and Adults With Duchenne Muscular Dystrophy Not Available Not Available approved_for_marketing NCT02167217
Historically Controlled Trial of Corticosteroids in Young Boys With Duchenne Muscular Dystrophy treatment 2 completed NCT01385917
Observational Study of Patients With Duchenne Muscular Dystrophy Theoretically Treatable With Exon 53 Skipping No drug interventions Not Available Not Available unknown_status NCT04173234
Aerobic Exercise in Duchenne Muscular Dystrophy No drug interventions treatment Not Available completed NCT02891434
Analysis of a Virtual Reality Task in Patients With Duchenne Muscular Dystrophy No drug interventions supportive_care Not Available completed NCT02241434
Stem Cell Therapy in Duchenne Muscular Dystrophy No drug interventions treatment 1 withdrawn NCT02376816
Clinical Intramuscular Gene Transfer Trial of rAAVrh74.MCK.Micro-Dystrophin to Patients With Duchenne Muscular Dystrophy No drug interventions treatment 1 completed NCT03354039
Tamoxifen in Duchenne Muscular Dystrophy treatment 3 completed NCT01396239
Efficacy Study of AVI-4658 to Induce Dystrophin Expression in Selected Duchenne Muscular Dystrophy Patients treatment 2 completed NCT02081625
Exploratory Study of NS-065/NCNP-01 in DMD treatment 1 completed NCT06174025
Validity and Reliability of the 6 Minute Pegboard Ring Test No drug interventions Not Available Not Available completed NCT02994030
Biomarker for Duchenne Muscular Dystrophy No drug interventions Not Available Not Available completed NCT05575648
Dual Task in Duchenne Muscular Dystrophy No drug interventions diagnostic Not Available completed NCT02819557
Study of Ataluren in ≥2 to <5 Year-Old Male Participants With Duchenne Muscular Dystrophy treatment 2 completed NCT01633866
Pediatric Radio Frequency Coils Generic No drug interventions Not Available Not Available active_not_recruiting NCT01826474
Phase IIb Study of PRO045 in Subjects With Duchenne Muscular Dystrophy treatment 1 / 2 terminated NCT00005574
Gentamicin Treatment of Muscular Dystrophy treatment 1 completed NCT06564974
Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy. Not Available Not Available recruiting NCT04687020
Long-term Use of Viltolarsen in Boys With Duchenne Muscular Dystrophy in Clinical Practice (VILT-502) treatment 4 active_not_recruiting NCT04287582
The Evaluation of Muscle Activation in Climbing up Stairs Activity in Children With Duchenne Muscular Dystrophy No drug interventions Not Available Not Available unknown_status NCT01847573
Safety, Tolerability, and Pharmacokinetics of Single and Multiple Doses of HT-100 in Duchenne Muscular Dystrophy treatment 1 / 2 terminated NCT03589573
Effect of Muscle Strength on Hamstring Flexibility in Children With Duchenne Muscular Dystrophy No drug interventions Not Available Not Available completed NCT02285673
Efficacy of Umbilical Cord Mesenchymal Stem Cells in Duchenne Muscular Dystrophy No drug interventions treatment 1 / 2 unknown_status NCT06491927
Long Term Follow-up for RGX-202 No drug interventions Not Available Not Available enrolling_by_invitation NCT03648827
A Study to Assess Dystrophin Levels in Participants With Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD) treatment 2 completed NCT00759876
Phase 2a Extension Study of Ataluren (PTC124) in Duchenne Muscular Dystrophy (DMD) treatment 2 terminated NCT04428476
Open-label Extension of the HOPE-2 Trial treatment 2 active_not_recruiting NCT02484560
Efficacy of Stem Cell Therapy in Ambulatory and Non-ambulatory Children With Duchenne Muscular Dystrophy - Phase 1-2 No drug interventions treatment 1 unknown_status NCT03689660
Feasibility of Virtual Reality in Children With Neuromuscular Disease, Effectiveness of Virtual Reality and Biofeedback No drug interventions treatment Not Available unknown_status NCT01009294
Study of Ataluren (PTC124) in Nonambulatory Participants With Nonsense-Mutation-Mediated Duchenne/Becker Muscular Dystrophy (nmDMD/BMD) treatment 2 terminated NCT03936894
Single Escalating Dose Pilot Trial of Canakinumab (ILARIS®) in Duchenne Muscular Dystrophy treatment 1 / 2 active_not_recruiting NCT05564962
Quality and Independence of Gait Classification Scale for DMD (QIGS-DMD) No drug interventions Not Available Not Available completed NCT01081080
Cardiac Magnetic Resonance in Children With Muscular Dystrophy No drug interventions Not Available Not Available completed NCT02972580
Characterization of Clinical Skeletal and Cardiac Impairment in Carriers of DMD and BMD No drug interventions Not Available Not Available active_not_recruiting NCT03760029
A Natural History Study In Chinese Male Patients With Duchenne Muscular Dystrophy No drug interventions other Not Available completed NCT04956289
Study to Assess the Safety, Tolerability, and Efficacy of Viltolarsen in Ambulant and Non-Ambulant Boys With DMD (Galactic53) treatment 2 completed NCT02780492
Outcome Measures in Duchenne Muscular Dystrophy: A Natural History Study No drug interventions Not Available Not Available completed NCT03529240
Kinesiology Taping in Duchenne Muscular Dystrophy: Effects on Performance, Gait Characteristics, and Energy Consumption No drug interventions supportive_care Not Available completed NCT04632940
Phase 3 Trial of Pamrevlumab or Placebo in Combination With Systemic Corticosteroids in Participants With Ambulatory DMD treatment 3 terminated NCT01610440
Safety and Efficacy of Umbilical Cord Mesenchymal Stem Cell Therapy for Patients With Duchenne Muscular Dystrophy treatment 1 / 2 unknown_status NCT01183767
Sunphenon Epigallocatechin-Gallate (EGCg) in Duchenne Muscular Dystrophy treatment 2 / 3 completed NCT02196467
Transplantation of Myoblasts to Duchenne Muscular Dystrophy (DMD) Patients No drug interventions treatment 1 / 2 unknown_status NCT01580501
PDE Inhibitors in DMD Study (Acute Dosing Study) treatment 1 completed NCT01540604
CRD007 for the Treatment of Duchenne Muscular Dystrophy, Becker Muscular Dystrophy and Symptomatic Carriers No drug interventions Not Available 2 completed NCT04972604
CureDuchenne Link®: A Resource for Research No drug interventions Not Available Not Available recruiting NCT04120168
Study Determining the Frequency of Duchenne Muscular Dystrophy and Late-onset Pompe Disease No drug interventions Not Available Not Available completed NCT00110669
High-dose Prednisone in Duchenne Muscular Dystrophy treatment 3 completed NCT02329769
Open Label, Extension Study of PRO044 in Duchenne Muscular Dystrophy (DMD) treatment 2 terminated NCT06539169
FLOWER: Following Longitudinal Outcomes With Epidemiology for Rare Diseases No drug interventions Not Available Not Available recruiting NCT01521546
Eplerenone for Subclinical Cardiomyopathy in Duchenne Muscular Dystrophy treatment Not Available completed NCT00004646
Phase III Randomized, Double-Blind Study of Prednisone for Duchenne Muscular Dystrophy treatment 3 completed NCT05464446
Examination of Lower Urinary System Symptoms With Duchenne Muscular Dystrophy No drug interventions Not Available Not Available completed NCT03589612
Regression of Hamstring Flexibility and Performance in Children With Duchenne Muscular Dystrophy No drug interventions Not Available Not Available completed NCT05436210
Postural and Anthropometric Properties of Foot and Ankle of Patients With DMD No drug interventions Not Available Not Available completed NCT05244395
Development of a New Instrument to Evaluate Gait Characteristics of Individuals With Duchenne Muscular Dystrophy No drug interventions other Not Available completed NCT03218995
Study of Eteplirsen in Young Participants With Duchenne Muscular Dystrophy (DMD) Amenable to Exon 51 Skipping treatment 2 completed NCT04240314
AAV9 U7snRNA Gene Therapy to Treat Boys With DMD Exon 2 Duplications. treatment 1 / 2 active_not_recruiting NCT02168114
Magnetic Resonance and Optical Imaging of Dystrophic and Damaged Muscle No drug interventions diagnostic Not Available completed NCT03372655
Prognostic Factors Affecting Duchenne Muscular Dystrophy No drug interventions Not Available Not Available unknown_status NCT01066455
Cardiac Outcome Measures in Children With Muscular Dystrophy No drug interventions Not Available Not Available completed NCT05274555
Reliability and Validity of the Turkish Version of the Upper Limb Short Questionnaire in Duchenne Muscular Dystrophy No drug interventions Not Available Not Available completed NCT01491555
Electrical Impedance Myography and Ultrasound as Biomarkers of Duchenne Muscular Dystrophy No drug interventions Not Available Not Available completed NCT00159250
Safety and Efficacy Study of Antisense Oligonucleotides in Duchenne Muscular Dystrophy treatment 1 / 2 completed NCT05938023
A Study of ATL1102 or Placebo in Participants With Non-ambulatory Duchenne Muscular Dystrophy treatment 2 active_not_recruiting NCT03655223
Early Check: Expanded Screening in Newborns No drug interventions Not Available Not Available enrolling_by_invitation NCT01168908
Revatio for Heart Disease in Duchenne Muscular Dystrophy and Becker Muscular Dystrophy treatment 2 terminated NCT05016908
Extracellular RNA Biomarkers of Duchenne Muscular Dystrophy No drug interventions Not Available Not Available recruiting NCT01207908
Safety and Efficacy Study of IGF-1 in Duchenne Muscular Dystrophy treatment 1 / 2 completed NCT02418338
2D Strain Evaluation: Children With Duchenne Muscular Dystrophy Versus Healthy Children No drug interventions diagnostic Not Available completed NCT05657938
Evaluation of Home Based Assessments on Participants With DMD No drug interventions Not Available Not Available completed NCT02485938
HOPE-Duchenne (Halt cardiomyOPathy progrEssion in Duchenne) treatment 1 / 2 completed NCT01772043
Duchenne Muscular Dystrophy Tissue Bank for Exon Skipping No drug interventions Not Available Not Available unknown_status NCT05996003
NS-089/NCNP-02-201 in Boys With Duchenne Muscular Dystrophy (DMD) treatment 2 recruiting NCT03333590
Gene Transfer Clinical Trial to Deliver rAAVrh74.MCK.GALGT2 for Duchenne Muscular Dystrophy treatment 1 / 2 active_not_recruiting NCT02760264
A Study to Assess Vamorolone in Boys With Duchenne Muscular Dystrophy (DMD) treatment 2 completed NCT05689164
A Study to Understand the Long-term Safety and Effects of an Experimental Gene Therapy for Duchenne Muscular Dystrophy. other 3 recruiting NCT05096221
A Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) No drug interventions treatment 3 active_not_recruiting NCT02958202
Extension Study of BMN 044 in Duchenne Muscular Dystrophy (DMD) treatment 2 terminated NCT03362502
A Study to Evaluate the Safety and Tolerability of PF-06939926 Gene Therapy in Duchenne Muscular Dystrophy No drug interventions treatment 1 active_not_recruiting NCT04384354
Digestive Events in Duchenne Muscular Dystrophy Patients No drug interventions Not Available Not Available completed NCT04740554
Heart Rate Variability in Individuals With Duchenne Muscular Dystrophy No drug interventions Not Available Not Available completed NCT02964377
Plus Epicatechin Duchenne Muscular Dystrophy in Non-ambulatory Adolescents treatment 1 / 2 completed NCT00312247
Biomechanical Analysis of Gait in Individuals With Duchenne Muscular Dystrophy No drug interventions Not Available Not Available completed NCT05712447
Duchenne Muscular Dystrophy Video Assessment Registry No drug interventions Not Available Not Available recruiting NCT01645098
Sedation During Muscle Biopsy in Patients With Duchenne Muscular Dystrophy treatment Not Available completed NCT02034305
Peak Cough Flow and Cough Clearance in Patients With Muscular Dystrophy No drug interventions Not Available Not Available completed NCT00844597
Dose-Ranging Study of AVI-4658 to Induce Dystrophin Expression in Selected Duchenne Muscular Dystrophy (DMD) Patients treatment 1 / 2 completed NCT02851797
Clinical Study to Evaluate the Efficacy and Safety of Givinostat in Ambulant Patients With Duchenne Muscular Dystrophy treatment 3 completed NCT05249361
Correlation Between Functional Capacity and Functional Capability in Duchenne Muscular Dystrophy No drug interventions Not Available Not Available recruiting NCT01099761
Study of ACE-031 in Subjects With Duchenne Muscular Dystrophy treatment 2 terminated NCT06412328
Psychoeducation Program for Parents of Children With DMD No drug interventions supportive_care Not Available completed NCT03521271
Investigation Of Factors Affecting Hand Functions in Nonambulatory Patients With Duchenne Muscular Dystrophy No drug interventions Not Available Not Available completed NCT05661071
Neuropsychological Profiles of Children With Duchenne Muscular Dystrophy and Its Effects on Motor Functions No drug interventions Not Available Not Available active_not_recruiting NCT06054971
NSAA NON-Interventional Study Protocol No drug interventions Not Available Not Available recruiting NCT04012671
A Registered Cohort Study on Duchenne Muscular Dystrophy No drug interventions Not Available Not Available recruiting NCT01484678
Magnetic Resonance Imaging and Biomarkers for Muscular Dystrophy No drug interventions Not Available Not Available recruiting NCT03985878
A Study to Evaluate Safety, Tolerability, and Efficacy of Eteplirsen in Participants With Duchenne Muscular Dystrophy (DMD) Who Have Completed Study 4658-102 (NCT03218995) treatment 2 terminated NCT03603288
Phase III Study With Idebenone in Patients With Duchenne Muscular Dystrophy (SIDEROS-E) treatment 3 terminated NCT03531788
Use of Dynamic Arm Supports to Promote Activities of Daily Living in Individuals With DMD No drug interventions treatment Not Available terminated NCT01603407
Finding the Optimum Regimen for Duchenne Muscular Dystrophy treatment 3 completed NCT03433807
Expanded Access Program for Idebenone in Participants With Duchenne Muscular Dystrophy (DMD) Not Available Not Available no_longer_available NCT01125709
Comparative Study of Clinical Endpoint in DMD: Handheld Myometry (HHM) Versus CINRG Quantitative Measurement System (CQMS) No drug interventions Not Available Not Available completed NCT02069756
The Duchenne Registry No drug interventions Not Available Not Available recruiting NCT06114056
A Clinical Study Evaluating the Safety, Tolerability, and Initial Efficacy of Single Intravenous Infusion of JWK007 in Patients With Duchenne Muscular Dystrophy (DMD) No drug interventions treatment 1 recruiting NCT04281485
Study to Evaluate the Safety and Efficacy of PF-06939926 for the Treatment of Duchenne Muscular Dystrophy No drug interventions treatment 3 active_not_recruiting NCT02516085
Improved Muscle Function in Duchenne Muscular Dystrophy Through L-Arginine and Metformin treatment 1 completed NCT06445985
Hydrotherapy in Duchenne Muscular Dystrophy (DMD) No drug interventions supportive_care Not Available recruiting NCT04193085
Wearable Technology to Assess Gait Function in SMA and DMD No drug interventions Not Available Not Available completed NCT03443115
Duchenne Muscular Dystrophy Heart Study No drug interventions Not Available Not Available unknown_status NCT03796637
A Study to Assess Dystrophin Levels in Participants With Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD) Who Have Been Treated With Ataluren other 2 completed NCT06579352
Expanded Access Study of UC-MSC in DMD Patients Not Available Not Available available NCT02354352
Therapeutic Potential for Aldosterone Inhibition in Duchenne Muscular Dystrophy treatment 3 completed NCT02251600
A Pharmacokinetic Study of Oral Deflazacort in Children and Adolescent Subjects With Duchenne Muscular Dystrophy basic_science 1 completed NCT03836300
Parent and Infant Inter(X)Action Intervention (PIXI) No drug interventions treatment Not Available enrolling_by_invitation NCT01557400
Study of Ataluren for Previously Treated Participants With Nonsense Mutation Duchenne/Becker Muscular Dystrophy (nmDBMD) in Europe, Israel, Australia, and Canada treatment 3 completed NCT06579859
Development of a Registry to Assess Natural History in Duchenne Muscular Dystrophy No drug interventions Not Available Not Available not_yet_recruiting NCT01874275
Duchenne Muscular Dystrophy Clinical Trial No drug interventions treatment Not Available completed NCT05195775
Tadalafil as Adjuvant Therapy for DMD treatment 2 / 3 recruiting NCT03439670
A Study to Assess the Efficacy and Safety of Vamorolone in Boys With Duchenne Muscular Dystrophy (DMD) treatment 2 completed NCT01359670
Tadalafil and Sildenafil for Duchenne Muscular Dystrophy treatment 0 completed NCT03368742
Microdystrophin Gene Transfer Study in Adolescents and Children With DMD No drug interventions treatment 1 / 2 active_not_recruiting NCT05514249
Treatment of a Single Patient With CRD-TMH-001 No drug interventions treatment 1 unknown_status NCT02606136
Trial of Pamrevlumab (FG-3019), in Non-Ambulatory Participants With Duchenne Muscular Dystrophy (DMD) treatment 2 terminated NCT05558813
Natural History of Duchenne Muscular Dystrophy Cardiomyopathy (DMD-CMP) No drug interventions diagnostic Not Available not_yet_recruiting NCT00308113
CoQ10 and Prednisone in Non-Ambulatory DMD treatment 3 terminated NCT06295718
Tele-assessment of Functional Performance and Quality of Life in Patients With Duchenne Muscular Dystrophy: Validity and Reliability Study No drug interventions Not Available Not Available enrolling_by_invitation NCT03863119
Expanded Access Protocol for Boys With Duchenne Muscular Dystrophy Not Available Not Available available NCT06270719
An Observational Study Comparing Delandistrogene Moxeparvovec With Standard of Care in Participants With Duchenne Muscular Dystrophy No drug interventions Not Available Not Available recruiting NCT03917719
An Open-Label Extension Study of Edasalonexent in Boys With Duchenne Muscular Dystrophy treatment 3 terminated NCT04583917
Brain Involvement in Dystrophinopathies Part 1 No drug interventions Not Available Not Available completed NCT04433234
Long-term, Extension Study of DS-5141b in Patients With Duchenne Muscular Dystrophy treatment 2 active_not_recruiting NCT01648634
Nebivolol for the Prevention of Left Ventricular Systolic Dysfunction in Patients With Duchenne Muscular Dystrophy prevention 3 completed NCT04607824
Heart Rate Variability in Duchenne Muscular Dystrophy During Computer Task No drug interventions Not Available Not Available completed NCT01182324
The PTC124 (Ataluren) Clinical Trial for Duchenne Muscular Dystrophy: Exploration of the Experiences of Parents, Clinician Researchers, and the Industry Sponsor No drug interventions Not Available Not Available completed NCT04668716
Brain Involvement in Dystrophinopathies Part 2 No drug interventions Not Available Not Available completed NCT06124196
Wearable Technology to Evaluate Hyperglycemia and HRV in DMD No drug interventions Not Available Not Available recruiting NCT01239758
Extension Study of ACE-031 in Subjects With Duchenne Muscular Dystrophy treatment 2 terminated NCT03558958
Safety and Efficacy of P-188 NF in DMD Patients No drug interventions treatment 2 terminated NCT00428935
Safety Study of Mini-dystrophin Gene to Treat Duchenne Muscular Dystrophy No drug interventions treatment 1 completed NCT02310763
A Phase 2 Study to Evaluate the Safety, Efficacy, Pharmacokinetics and Pharmacodynamics of PF-06252616 in Duchenne Muscular Dystrophy treatment 2 terminated NCT05601986
Motor Imagery on Children With DMD on Gait and Balance Functions No drug interventions supportive_care Not Available recruiting NCT02636686
Extension Study of Drisapersen in DMD Subjects Not Available Not Available no_longer_available NCT03039686
Clinical Trial to Evaluate the Efficacy, Safety, and Tolerability of RO7239361 in Ambulatory Boys With Duchenne Muscular Dystrophy treatment 2 / 3 completed NCT05019625
Biomarker Development for Muscular Dystrophies No drug interventions Not Available Not Available recruiting NCT06328725
Evaluate the Efficacy and Safety of EN001 in Patients With Duchenne Muscular Dystrophy treatment 1 / 2 not_yet_recruiting NCT00758225
Long-term Safety, Tolerability and Efficacy of Idebenone in Duchenne Muscular Dystrophy (DELPHI Extension) treatment 2 completed NCT02704325
Gene Transfer Clinical Trial for Duchenne Muscular Dystrophy Using rAAVrh74.MCK.GALGT2 treatment 1 / 2 withdrawn NCT05280730
Assessment of Neurodevelopmental Needs in Duchenne Muscular Dystrophy No drug interventions Not Available Not Available recruiting NCT03319030
Aerobic Exercise in Boys With Duchenne Muscular Dystrophy (DMD) No drug interventions Not Available Not Available completed NCT02752048
A Phase IIa Study of TAS-205 for Duchenne Muscular Dystrophy No drug interventions treatment 2 completed NCT02295748
An Open-Label, Long-Term Extension Study to Evaluate the Safety and Tolerability Deflazacort treatment 1 completed NCT04371666
Phase 3 Trial of Pamrevlumab or Placebo With Systemic Corticosteroids in Participants With Non-ambulatory Duchenne Muscular Dystrophy (DMD) treatment 3 terminated NCT01978366
Open Label Extension Study of HT-100 in Patients With DMD treatment 2 terminated NCT03680365
Your Voice; Impact of Duchenne Muscular Dystrophy (DMD) on the Lives of Families No drug interventions Not Available Not Available completed NCT06540365
Applying the Pathways and Resources for Engagement and Participation Protocol Among People With Muscles Dystrophies No drug interventions treatment Not Available not_yet_recruiting NCT00451074
Six Month Study of Gentamicin in Duchenne Muscular Dystrophy With Stop Codons treatment 1 completed NCT03552874
Pulmonary and Upper Limb Functions in Duchenne Muscular Dystrophy No drug interventions Not Available Not Available completed NCT02436720
Upper Limb Assessment in Duchenne Muscular Dystrophy No drug interventions Not Available Not Available unknown_status NCT05281120
Effects of Low-level Mechanical Vibration on Bone Density in Ambulant Children Affected by Duchenne Muscular Dystrophy No drug interventions treatment Not Available completed NCT03067831
Bone Marrow-Derived Autologous Stem Cells for the Treatment of Duchenne Muscular Dystrophy No drug interventions treatment 1 / 2 unknown_status NCT03882827
Natural History of Duchenne Muscular Dystrophy No drug interventions Not Available Not Available unknown_status NCT05305976
Telerehabilitation in Duchenne Muscular Dystrophy No drug interventions prevention Not Available completed NCT04906460
Open-label Study of WVE-N531 in Patients With Duchenne Muscular Dystrophy (FORWARD-53) treatment 1 / 2 active_not_recruiting NCT05412394
Once Weekly Infant Corticosteroid Trial for DMD treatment 4 recruiting NCT04129294
Exploratory Study of NS-089/NCNP-02 in DMD No drug interventions treatment 1 / 2 completed NCT04768062
Study to Assess the Safety and Efficacy of Viltolarsen in Ambulant Boys With DMD (RACER53-X) treatment 3 active_not_recruiting NCT02858362
Proof of Concept Study to Assess Activity and Safety of SMT C1100 (Ezutromid) in Boys With Duchenne Muscular Dystrophy (DMD) treatment 2 terminated NCT05753462
Phase 1/2a for Safety, PK and PD of SQY51 in Paediatric and Adult Patients Duchenne Muscular Dystrophy No drug interventions other 1 / 2 recruiting NCT03611244
Prevention of Scoliosis in Patients With Duchenne Muscular Dystrophy Using Portable Seat Device No drug interventions prevention Not Available recruiting NCT01931644
At-Home Research Study for Patients With Autoimmune, Inflammatory, Genetic, Hematological, Infectious, Neurological, CNS, Oncological, Respiratory, Metabolic Conditions No drug interventions Not Available Not Available completed NCT01954940
Whole Body Vibration Therapy in Boys With Duchenne Muscular Dystrophy No drug interventions prevention Not Available completed NCT04782440
The Effect of Telerehabilitation of Patients With Duchenne Muscular Dystrophy No drug interventions supportive_care Not Available unknown_status NCT03513367
The Validation Process for Confirmation of the French Version of the Pediatric Quality of Life Inventory :PedsQLTM. No drug interventions Not Available Not Available unknown_status NCT01753804
A Prospective Natural History Study of Progression of Subjects With Duchenne Muscular Dystrophy. No drug interventions Not Available Not Available terminated NCT03907072
Efficacy and Safety Study of WVE-210201 (Suvodirsen) With Open-label Extension in Ambulatory Patients With Duchenne Muscular Dystrophy treatment 2 / 3 terminated NCT02740972
Safety and Dose Finding Study of NS-065/NCNP-01 in Boys With Duchenne Muscular Dystrophy (DMD) treatment 2 completed NCT03373968
Givinostat in Duchenne's Muscular Dystrophy Long-term Safety and Tolerability Study treatment 2 / 3 enrolling_by_invitation NCT03779646
Bisoprolol in DMD Early Cardiomyopathy treatment 2 / 3 unknown_status NCT03947112
Physical Activity Level of Norwegian Boys With Duchenne Muscular Dystrophy No drug interventions Not Available Not Available completed NCT05559710
Motor Imagery in Duchenne Muscular Dystrophy No drug interventions Not Available Not Available completed NCT02354781
Clinical Intramuscular Gene Transfer of rAAV1.CMV.huFollistatin344 Trial to Patients With Duchenne Muscular Dystrophy other 1 / 2 completed NCT01335295
Safety Study of Flavocoxid in Duchenne Muscular Dystrophy No drug interventions Not Available 1 completed NCT05330195
Bicycle Ergometer Training in Duchenne Muscular Dystrophy No drug interventions treatment Not Available completed NCT04708314
An Open-Label Study of Golodirsen in Non-Ambulant Patients With Duchenne Muscular Dystrophy treatment 4 terminated NCT06053814
NS-050/NCNP-03 in Boys With DMD (Meteor50) No drug interventions treatment 1 / 2 not_yet_recruiting NCT03167255
Extension Study of NS-065/NCNP-01 in Boys With Duchenne Muscular Dystrophy (DMD) treatment 2 completed NCT06241950
A Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of Delandistrogene Moxeparvovec (SRP-9001) Following Imlifidase Infusion in Participants With Duchenne Muscular Dystrophy (DMD) Determined to Have Pre-existing Antibodies to Recombinant Adeno-Associated Virus Serotype (rAAVrh74) treatment 1 enrolling_by_invitation NCT02421523
Strength Training in Duchenne Muscular Dystrophy No drug interventions health_services_research Not Available completed NCT02340923
A Device for Rapid, Painless, Bedside Muscle Evaluation of Children No drug interventions Not Available Not Available completed NCT02056808
A Phase 1b Study of SMT C1100 in Subjects With Duchenne Muscular Dystrophy (DMD) treatment 1 completed NCT04587908
A Phase 3 Study of TAS-205 in Patients With Duchenne Muscular Dystrophy(REACH-DMD) No drug interventions treatment 3 active_not_recruiting NCT01098708
This is a Study to Get More Information About Non Ambulatory Boys & Men With Duchenne Muscular Dystrophy No drug interventions Not Available Not Available completed NCT01995032
L-citrulline and Metformin in Duchenne's Muscular Dystrophy treatment 3 completed NCT02369731
Registry of Translarna (Ataluren) in Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD) No drug interventions Not Available Not Available active_not_recruiting NCT01918384
Phase II Study of NPC-14 (Arbekacin Sulfate) to Explore Safety, Tolerability, and Efficacy in Duchenne Muscular Dystrophy treatment 2 unknown_status NCT01027884
Phase III Study of Idebenone in Duchenne Muscular Dystrophy (DMD) treatment 3 completed NCT01865084
A Study of Tadalafil for Duchenne Muscular Dystrophy treatment 3 terminated NCT05209087
Effects of Parental Influence on Physical Activity Level and Participation in Children With Duchenne Muscular Dystrophy No drug interventions Not Available Not Available completed NCT03963453
Regular Physical Exercise in Duchenne Muscular Dystrophy No drug interventions Not Available Not Available completed NCT00102453
Pentoxifylline in Duchenne Muscular Dystrophy treatment 1 / 2 completed NCT04669847
The Effects of Trunk Exercises on Upper Extremity and Respiratory Functions in DMD No drug interventions treatment Not Available completed NCT00033813
KUL0401: An Open-label Pilot Study of Oxatomide in Steroid-Naive Duchenne Muscular Dystrophy treatment 2 completed NCT01506518
Double Push Acoustic Radiation Force (DP ARF) Ultrasound for Monitoring Degeneration in Duchenne Muscular Dystrophy No drug interventions Not Available Not Available completed NCT03777319
Spironolactone Versus Prednisolone in DMD treatment 1 terminated NCT03789734
Safety Study of BLS-M22 in Healthy Volunteers treatment 1 completed NCT01826422
Effect of EPA and DHA in the Inflammation and Metabolic Disorders in DMD/DMB Patients No drug interventions prevention Not Available completed NCT03992430
A Study to Compare Safety and Efficacy of a High Dose of Eteplirsen in Participants With Duchenne Muscular Dystrophy (DMD) (MIS51ON) treatment 3 active_not_recruiting NCT03675126
An Open-Label Extension Study for Patients With Duchenne Muscular Dystrophy Who Participated in Studies of SRP-5051 (Vesleteplirsen) treatment 1 / 2 terminated NCT04626674
A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) No drug interventions treatment 1 active_not_recruiting NCT03703882
Phase III Study of Edasalonexent in Boys With Duchenne Muscular Dystrophy treatment 3 completed NCT02710591
Rimeporide in Patients With Duchenne Muscular Dystrophy treatment 1 completed NCT05429372
Study of Fordadistrogene Movaparvovec in Early Stage Duchenne Muscular Dystrophy No drug interventions treatment 2 active_not_recruiting NCT06147414
Development of Non-Invasive Prenatal Diagnosis for Single Gene Disorders No drug interventions Not Available Not Available not_yet_recruiting NCT03375255
A Study to Evaluate the Safety, Tolerability, and Pharmacokinetics of a Single Dose of SRP-5051 (Vesleteplirsen) in Patients With Duchenne Muscular Dystrophy (DMD) treatment 1 completed NCT00296621
Effect of Oral Glutamine on Muscle Mass and Function in Duchenne Muscular Dystrophy treatment 2 completed NCT05066633
The Efficacy and Safety of Metoprolol as add-on Treatment to Standard of Care in Preventing Cardiomyopathy in Patients With DMD treatment 3 recruiting NCT05833633
Study of Genotype and Phenotype Characterization in Duchenne Muscular Dystrophy With Small Mutations No drug interventions Not Available Not Available recruiting NCT00016653
Creatine and Glutamine in Steroid-Naive Duchenne Muscular Dystrophy treatment 2 / 3 completed NCT02286947
Safety Study of Eteplirsen to Treat Advanced Stage Duchenne Muscular Dystrophy treatment 2 completed NCT02383511
Modified Diet Trial: A Study of SMT C1100 in Paediatric Patients With DMD Who Follow a Balanced Diet treatment 1 completed NCT00018109
A Multicenter Randomized Placebo-Controlled Double-Blind Study to Assess Efficacy and Safety of Glutamine and Creatine Monohydrate in Duchenne Muscular Dystrophy (DMD) treatment 3 completed NCT03400852
A Study to Assess the Efficacy and Safety of MNK-1411 in Duchenne Muscular Dystrophy treatment 2 terminated NCT02195999
Assessment of Cardiopulmonary Function in Duchenne Muscular Dystrophy No drug interventions Not Available Not Available completed NCT03769116
A Randomized, Double-blind, Placebo-controlled Study of Delandistrogene Moxeparvovec (SRP-9001) for Duchenne Muscular Dystrophy (DMD) No drug interventions treatment 1 / 2 completed NCT02439216
Phase 1/2 Study in Boys With Duchenne Muscular Dystrophy treatment 1 / 2 completed NCT06363357
The Effect of a Muscle-mimicking, Fabric-type Shoulder Orthosis on Functional Movements of the Upper Limb in Patients With Duchenne Muscular Dystrophy No drug interventions supportive_care Not Available recruiting NCT00033189
An Open-label Pilot Study of Coenzyme Q10 in Steroid-Treated Duchenne Muscular Dystrophy treatment 2 completed NCT00243789
Study of Daily Pentoxifylline as a Rescue Treatment in Duchenne Muscular Dystrophy treatment 1 / 2 completed NCT06337669
Characterization of DupEx2 Duchenne Muscular Dystrophy No drug interventions Not Available Not Available recruiting NCT02834650
Validating Cardiac MRI Biomarkers and Genotype-Phenotype Correlations for DMD No drug interventions basic_science Not Available completed