Duchenne Muscular Dystrophy (DMD) (DBCOND0040032)

Identifiers

Synonyms
Muscular Dystrophy, Duchenne Type / DMD / Muscular Dystrophy / Muscular Dystrophies / Muscular Dystrophy (DMD) / Duchenne Muscular Distrophy (DMD) / Dystrophy, Muscular / Duchenne's Muscular Dystrophy / Duchenne Dystrophy Muscular / Duchenne Muscular Dystrophy / Duchenne's Muscular Dystrophy (DMD) / Muscular Dystrophy, Duchenne / Muscular dystrophy NOS / Muscular dystrophy (disorder) / Becker muscular dystrophy (disorder) / Duchenne muscular dystrophy (disorder)

Associated Data

Indicated Drugs and Targets
DrugDescriptionTargets
Ataluren
A medication used for the treatment of Duchenne muscular dystrophy.
Casimersen
An antisense phosphorodiamidate morpholino oligonucleotide used to treat Duchenne muscular dystrophy patients with mutations amenable to exon 45 skipping.
Deflazacort
A corticosteroid used to treat Duchenne muscular dystrophy.
Delandistrogene moxeparvovec
A gene therapy used to treat Duchenne Muscular Dystrophy in ambulatory children with DMD gene mutation.
No drug targets
Eteplirsen
An antisense oligonucleotide used to treat Duchenne muscular dystrophy (DMD) in patients with a confirmed mutation of the DMD gene that is amenable to exon 51 skipping.
Givinostat
A histone deacetylase inhibitor indicated for the treatment of Duchenne Muscular Dystrophy (DMD).
Golodirsen
A drug used to treat certain mutations that cause Duchenne muscular dystrophy (DMD).
Vamorolone
A synthetic glucocorticoid used as an anti-inflammatory and immunosuppressant in the management of Duchenne muscular dystrophy (DMD).
Viltolarsen
An antisense phosphorodiamidate morpholino oligonucleotide specific for exon 53 of the human DMD gene that is capable of inducing exon 53 skipping to produce a functional truncated dystrophin protein in Duchenne muscular dystrophy patients with specific underlying mutations.
Clinical Trials
IdentifierTitleDrug(s)PurposePhaseStatus
NCT05688072
Trunk Oriented Exercises Versus Whole-body Vibration for Duchenne Muscular DystrophyNo drug interventionstreatmentNot Availablecompleted
NCT06581887
Defining Outcome Measures for Behavioural and Emotional Problems in DystrophinopathiesNo drug interventionsNot AvailableNot Availablerecruiting
NCT03649919
Multi-center Clinical Study on the Diagnosis and Treatment Management of Rare Neurological Disease in ChildrenNo drug interventionsNot AvailableNot Availablewithdrawn
NCT05102916
Swiss Registry for Neuromuscular DisordersNo drug interventionsNot AvailableNot Availablerecruiting
NCT01890616
Constipation and Gut Transit in DMD PatientsNo drug interventionsNot AvailableNot Availablecompleted
NCT05635266
Tissue Repository Providing Annotated Biospecimens for Approved Investigator-directed Biomedical Research InitiativesNo drug interventionsNot AvailableNot Availablerecruiting
NCT06290713
Vasodilator and Exercise Study for DMD (VASO-REx)treatment2recruiting
NCT06244082
Ph2 Open-label Study of AOC 1044 in Duchenne Muscular Dystrophy Participants With Mutations Amenable to Exon44 SkippingNo drug interventionstreatment2enrolling_by_invitation
NCT04337112
The Expanded Access Use of Viltolarsen in Duchenne Muscular Dystrophy With Confirmed Exon 53 Amenable MutationNot AvailableNot Availableapproved_for_marketing
NCT00313677
Clinical Trial Readiness for the DystroglycanopathiesNo drug interventionsNot AvailableNot Availablerecruiting
NCT04154098
Evaluation of a Textile Scapula OrthosisNo drug interventionsbasic_scienceNot Availablecompleted
NCT01950897
Muscle Tissue Bank for Muscular DystrophyNo drug interventionsNot AvailableNot Availablecompleted
NCT02241928
Stem Cell Therapy in Muscular DystrophyNo drug interventionstreatment1withdrawn
NCT01882400
Assessment of Response to Treatment of Osteoporosis With Oral Bisphosphonates in Patients With Muscular Dystrophyprevention4completed
NCT01633242
Heart Imaging in Children With Muscular DystrophyNo drug interventionsNot AvailableNot Availableterminated
NCT00912041
BrainGate2: Feasibility Study of an Intracortical Neural Interface System for Persons With TetraplegiaNo drug interventionsotherNot Availablerecruiting
NCT00518817
The Cardiovascular Genetic and Therapeutic Implications of Muscular DystrophyNo drug interventionsNot AvailableNot Availableunknown_status
NCT00138931
Genetics of Cardiovascular and Neuromuscular DiseaseNo drug interventionsNot AvailableNot Availablerecruiting
NCT05237973
Investigational Use of Neuromuscular UltrasoundNo drug interventionsNot AvailableNot Availablerecruiting
NCT01990976
Study of Morphology and Functional Magnetic Resonance Imaging (MRI) Muscle Patients With Muscular Dystrophy Type FSHD Benefiting a Physical Training Introduced.No drug interventionsNot AvailableNot Availablecompleted
NCT05726591
Evaluating Long-term Use of a Pediatric Robotic Exoskeleton (P.REX/Agilik) to Improve Gait in Children With Movement DisordersNo drug interventionsdevice_feasibilityNot Availablerecruiting
NCT01393444
ECoG Direct Brain Interface for Individuals With Upper Limb ParalysisNo drug interventionsNot AvailableNot Availablecompleted
NCT01834040
Study Safety and Efficacy of BMMNC for the Patient With Duchenne Muscular DystrophyNo drug interventionstreatment1 / 2unknown_status
NCT04035967
Investigation of Parents' Anxiety Level and Health Related Quality of Life in Different Types of Physical DisabilitiesNo drug interventionsNot AvailableNot Availablecompleted
NCT01451281
Studying Skeletal Muscle, Heart, and Diaphragm Imaging in Boys With Duchenne Muscular DystrophyNo drug interventionsNot AvailableNot Availablecompleted
NCT00082108
Myotonic Dystrophy and Facioscapulohumeral Muscular Dystrophy RegistryNo drug interventionsNot AvailableNot Availablerecruiting
NCT04038138
Clinical Trial Readiness Network FSHD France: Prospective 24 Months MRI StudyNo drug interventionsotherNot Availableactive_not_recruiting
NCT02104921
Innovative Ultrasound Technology in Neuromuscular DiseaseNo drug interventionsNot AvailableNot Availablecompleted
NCT02653833
The Study of Skeletal Muscle Blood Flow in Becker Muscular Dystrophybasic_science0terminated
NCT00622453
Arrhythmias in Myotonic Muscular DystrophyNo drug interventionsNot AvailableNot Availablecompleted
NCT05228405
Awareness Levels of Caregivers of Disabled ChildrenNo drug interventionsNot AvailableNot Availablecompleted
NCT04461561
Using NPT to Evaluate Providing PPC as ELNEC-PPC WBT for NursesNo drug interventionsotherNot Availableunknown_status
NCT03840928
PatientSpot Formerly Known as ArthritisPowerNo drug interventionsNot AvailableNot Availablerecruiting
NCT02218593
WREX Outcome StudyNo drug interventionsNot AvailableNot Availablecompleted
NCT01790178
Ultrasound in Muscle BiopsyNo drug interventionsNot AvailableNot Availablecompleted
NCT02815878
Enhance Wellness for Individuals With Long-Term Physical DisabilitiesNo drug interventionshealth_services_researchNot Availablecompleted
NCT05470478
iBCI Optimization for Veterans With ParalysisNo drug interventionsotherNot Availablenot_yet_recruiting
NCT02522507
A Peer E-mentoring Intervention to Improve EmploymentNo drug interventionstreatmentNot Availablecompleted
NCT05230459
A Study to Evaluate the Safety of AB-1003 (Previously LION-101) in Subjects With Genetic Confirmation of LGMD2I/R9 (Part1)No drug interventionstreatment1 / 2recruiting
NCT04574934
Effect of Aquatic Therapy on Pulmonary Functions in Patients With Muscular DystrophyNo drug interventionstreatmentNot Availableunknown_status
NCT02124616
National Registry for Egyptian Pediatric Neuromuscular DiseasesNo drug interventionsNot AvailableNot Availableunknown_status
NCT05644522
Nomad P-KAFO StudyNo drug interventionstreatmentNot Availablerecruiting
NCT05715957
Follow-up Study on Female Carriers With DMD Gene VariantsNo drug interventionsNot AvailableNot Availablenot_yet_recruiting
NCT01961557
Evaluating a New Knee-Ankle-Foot Brace to Improve Gait in Children With Movement DisordersNo drug interventionsdevice_feasibilityNot Availablerecruiting
NCT06363526
Effectiveness of 5-week Digital Respiratory Practice in a Group of Children With Duchenne Muscular Dystrophy and Becker Muscular Dystrophy.No drug interventionstreatmentNot Availablenot_yet_recruiting
NCT01834066
Study Safety and Efficacy of Bone Marrow Derived Autologous Cells for the Treatment of Muscular Dystrophy.No drug interventionstreatment1 / 2unknown_status
NCT02428673
Effects of Standing on Non-Ambulatory Children With Neuromuscular ConditionsNo drug interventionstreatmentNot Availablecompleted
NCT02532244
Genetics of Pediatric-Onset Motor Neuron and Neuromuscular DiseasesNo drug interventionsNot AvailableNot Availablerecruiting
NCT00004568
Study of Inherited Neurological DisordersNo drug interventionsNot AvailableNot Availablerecruiting
NCT00866112
A Randomized Exercise Trial for Wheelchair UsersNo drug interventionsNot AvailableNot Availablecompleted
NCT02745938
GDF-15 as a Biomarker for Mitochondrial DiseaseNo drug interventionsNot AvailableNot Availablecompleted
NCT00001164
Studies of Patients With Skin Disease, Patients With Neurological Degenerations, and Normal VolunteersNo drug interventionsNot AvailableNot Availablecompleted
NCT01459302
Genetic Study of Familial and Sporadic ALS/Motor Neuron Disease, Miyoshi Myopathy and Other Neuromuscular DisordersNo drug interventionsNot AvailableNot Availableenrolling_by_invitation
NCT01826487
Phase 3 Study of Ataluren in Participants With Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD)treatment3completed
NCT04798378
NuroSleeve Powered Brace & Stimulation System to Restore Arm FunctionNo drug interventionssupportive_careNot Availablerecruiting
NCT04694456
Pro-inflammatory Cytokines in Facioscapulohumeral Muscular Dystrophy (CYTOKINE-FSH)No drug interventionsotherNot Availablecompleted
NCT05730842
Absorption, Metabolism, Excretion and Absolute Bioavailability of EDG-5506 in Healthy Volunteerstreatment1completed
NCT04313049
LARA: Use of JACO2 Controlled by Joystick or by Voice Control System, in Muscular DystrophyNo drug interventionssupportive_careNot Availablecompleted
NCT01910649
A Phase I/II, Open Label, Escalating Dose, Pilot Study to Assess Effect, Safety, Tolerability and PK of Multiple SC Doses of Drisapersen in Patients With Duchenne Muscular Dystrophy and to Assess the Potential for IV Dosing as an Alternative Route of Administrationtreatment2terminated
NCT04392518
Telerehabilitation in Proximal Muscle WeaknessNo drug interventionstreatmentNot Availableunknown_status
NCT04468919
Optimizing BCI-FIT: Brain Computer Interface - Functional Implementation ToolkitNo drug interventionsbasic_scienceNot Availablerecruiting
NCT03127241
User-centred Assistive System for Arm Functions in Neuromuscular SubjectsNo drug interventionssupportive_careNot Availablecompleted
NCT04045158
Diaphragm Ultrasound in Neuromuscular DisordersNo drug interventionsNot AvailableNot Availableunknown_status
NCT02895763
Quality of Life in Neuromuscular DiseaseNo drug interventionsNot AvailableNot Availablecompleted
NCT03981289
Defining Clinical Endpoints in Limb Girdle Muscular Dystrophy (LGMD)No drug interventionsNot AvailableNot Availableactive_not_recruiting
NCT02109692
Evaluation of Muscle miRNA as Biomarkers in DystrophinopathiesNo drug interventionshealth_services_researchNot Availableunknown_status
NCT03951844
Wearability, Saefty and Usability Assessment for the Upper Limb Exoskeleton BRIDGE/EMPATIANo drug interventionsotherNot Availablecompleted
NCT05199246
Assessment of Safety and Acute Effects of a Lower-limb Powered Dermoskeleton in Patients With Neuromuscular DisordersNo drug interventionsotherNot Availablerecruiting
NCT01803412
A Study of the Safety, Tolerability & Efficacy of Long-term Administration of Drisapersen in US & Canadian Subjectstreatment3terminated
NCT04677010
Cycle Exercise in Wheelchair Users With Muscular Dystrophy or Cerebral PalsyNo drug interventionstreatmentNot Availablecompleted
NCT05479981
Extension of AOC 1001-CS1 (MARINA) Study in Adult Myotonic Dystrophy Type 1 (DM1) Patientstreatment2active_not_recruiting
NCT04313595
Device for Breathing Frequency Monitoring in Muscular DystrophyNo drug interventionssupportive_careNot Availablecompleted
NCT03490214
Non-invasive Imaging of Muscle Structure in Duchenne Muscular Dystrophy Using Multispectral Optoacoustic TomographyNo drug interventionsdiagnosticNot Availablecompleted
NCT01128855
A Double-blind, Escalating Dose, Randomized, Placebo-controlled Study Assessing PK, Safety, Tolerability in Non-ambulant DMD Subjectstreatment1completed
NCT05035823
COMMAND Early Feasibility Study: Implantable BCI to Control a Digital Device for People With ParalysisNo drug interventionsdevice_feasibilityNot Availableactive_not_recruiting
NCT04009408
Expiratory Muscle Strength Training (EMST) in Neuromuscular DisordersNo drug interventionstreatmentNot Availableunknown_status
NCT00674843
The Efficacy of Using Far Infrared Radiation to Manage Muscular DystrophiesNo drug interventionstreatment1unknown_status
NCT06378203
Rehabilitation in Muscular Dystrophies From the Hospital Facility to the Home: Pilot Project [RIMUDI]No drug interventionstreatmentNot Availablerecruiting
NCT05200702
Assessment of Safety and Acute Effects of a Knee-hip Powered Soft Exoskeleton in Patients With Neuromuscular DisordersNo drug interventionsotherNot Availablerecruiting
NCT05409079
Schulze Muscular Dystrophy Ability Clinical StudyNo drug interventionstreatmentNot Availablerecruiting
NCT04308447
Ablelite Pediatric Device Clinical StudyNo drug interventionstreatmentNot Availableunknown_status
NCT01480245
Open Label Study of GSK2402968 in Subjects With Duchenne Muscular Dystrophytreatment3terminated
NCT01890798
Drisapersen Duchenne Muscular Dystrophy (DMD) Treatment Protocoltreatment3withdrawn
NCT06094205
Feasibility of the BrainGate2 Neural Interface System in Persons With Tetraplegia (BG-Speech-02)No drug interventionsotherNot Availablerecruiting
NCT03508583
Turkish Version of The Measure of Processes of Care (MPOC)No drug interventionsNot AvailableNot Availableunknown_status
NCT03930628
Limb-Girdle Muscular Dystrophy Type 2I in NorwayNo drug interventionsNot AvailableNot Availableactive_not_recruiting
NCT03986671
Transmembrane Electromyography (TM-EMG) for the Assessment of Neuromuscular Function in the OropharynxNo drug interventionsdiagnosticNot Availablecompleted
NCT03317171
Safety and Efficacy of a Flavonoids- and omega3s-based Compound for the Treatment of Muscular DystrophiesNo drug interventionstreatmentNot Availablecompleted
NCT03851107
The Effectiveness of Participation-focused Interventions on Body Functions of Youth With Physical DisabilitiesNo drug interventionstreatmentNot Availablecompleted
NCT02432885
Myocardial Fibrosis Progression in Duchenne and Becker Muscular Dystrophy - ACE Inhibitor Therapy Trialtreatment3completed
NCT02685215
Prognostic Factors , Morbidity and Mortality in Patients With Neuromuscular Disorders Admitted in ICUNo drug interventionsNot AvailableNot Availableunknown_status
NCT06507215
Dysferlinopathy Protein in Peripheral Blood Monocytes.No drug interventionsNot AvailableNot Availablecompleted
NCT01153932
Phase II Doubleblind Exploratory Study of GSK2402968 in Ambulant Subjects With Duchenne Muscular Dystrophytreatment2completed
NCT02090959
An Extension Study of Ataluren (PTC124) in Participants With Nonsense Mutation Dystrophinopathytreatment3terminated
NCT02641275
Self-management Training for Parents With Chronic Muscular DystrophiaNo drug interventionssupportive_careNot Availablewithdrawn
NCT04525742
COVID-19 Pandemic and Parents of Disabled ChildrenNo drug interventionsscreeningNot Availablecompleted
NCT03698149
ECoG BMI for Motor and Speech ControlNo drug interventionsdevice_feasibilityNot Availablerecruiting
NCT01254019
A Clinical Study to Assess the Efficacy and Safety of GSK2402968 in Subjects With Duchenne Muscular Dystrophytreatment3completed
NCT05492734
A Study to Assess the Feasibility of Non-invasive Dried Blood Samplingtreatment1completed
NCT05747924
Phase 1/2 Study of AOC 1020 in Adults With Facioscapulohumeral Muscular Dystrophy (FSHD)treatment1 / 2recruiting
NCT06547216
Phase 2 Open-label Extension Study of AOC 1020 in Adults With Facioscapulohumeral Muscular Dystrophy (FSHD)treatment2enrolling_by_invitation
NCT05126758
A Study of CAP-1002 in Ambulatory and Non-Ambulatory Patients With Duchenne Muscular Dystrophytreatment3recruiting
NCT01568658
Genetic and Physical Study of Childhood Nerve and Muscle DisordersNo drug interventionsNot AvailableNot Availablerecruiting
NCT02315339
European Home Mechanical Ventilation RegistryNo drug interventionsNot AvailableNot Availableterminated
NCT05881122
Anti-inflammatory Diet Consultation for Those With Neuromuscular DisabilityNo drug interventionssupportive_careNot Availablecompleted
NCT00873782
Safety Study of Transvenous Limb Perfusion in Human Muscular DystrophyNo drug interventionstreatment1completed
NCT04187482
Myotonic Dystrophy Type 1 Aerobic Exercise StudyNo drug interventionssupportive_careNot Availablecompleted
NCT03179631
Long-Term Outcomes of Ataluren in Duchenne Muscular Dystrophytreatment3completed
NCT05257473
Defining Endpoints in Becker Muscular DystrophyNo drug interventionsNot AvailableNot Availablerecruiting
NCT05724173
Feasibility of the BrainGate2 Neural Interface System in Persons With TetraplegiaNo drug interventionsotherNot Availablerecruiting
NCT04202627
Biomarker Development in LGMD2iNo drug interventionsNot AvailableNot Availablecompleted
NCT04733976
Bullying in Youth With Muscular Dystrophy and Congenital MyopathiesNo drug interventionsNot AvailableNot Availablecompleted
NCT03627494
First Time in Human (FTIH) Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of Single and Repeat Doses of GSK3439171A in Healthy Subjects and to Assess Food EffectNo drug interventionstreatment1completed
NCT00027391
Study of Albuterol and Oxandrolone in Patients With Facioscapulohumeral Dystrophy (FSHD)treatmentNot Availablecompleted
NCT05081791
Exercise Therapy for Patients With Muscle DystrophiesNo drug interventionstreatmentNot Availablerecruiting
NCT03406780
A Study of CAP-1002 in Ambulatory and Non-Ambulatory Patients With Duchenne Muscular Dystrophytreatment2completed
NCT01462292
A Clinical Study to Assess Two Doses of GSK2402968 in Subjects With Duchenne Muscular Dystrophy (DMD)treatment2completed
NCT03811301
[BrainConnexion] - Neurodevice Phase I TrialNo drug interventionsotherNot Availableactive_not_recruiting
NCT01800604
Power Over Pain (POP) StudyNo drug interventionstreatmentNot Availablecompleted
NCT00494195
Gene Transfer Therapy for Treating Children and Adults With Limb Girdle Muscular Dystrophy Type 2D (LGMD2D)No drug interventionstreatment1completed
NCT05041114
SWITCH II Early Feasibility Study: Implantable BCI to Control a Digital Device for People With ParalysisNo drug interventionstreatmentNot Availablewithdrawn
NCT02921321
Pilot Study of Cardiac MR in Patients With Muscular DystrophyNo drug interventionsNot AvailableNot Availableactive_not_recruiting
NCT05945784
Exploring Accessible Beauty for Individuals With Upper Extremity DeficitsNo drug interventionsNot AvailableNot Availablecompleted
NCT02515669
Study of an Investigational Drug, RO7239361 (BMS-986089), in Ambulatory Boys With DMDbasic_science1 / 2terminated
NCT01823783
Endomysial Fibrosis, Muscular Inflammatory Response and Calcium Homeostasis Dysfunction in Duchenne Muscular DystrophyNo drug interventionsbasic_scienceNot Availableunknown_status
NCT03507530
Effects of Fear of Falling on Physical Performance and Quality of Life in Children With Duchenne Muscular DystrophyNo drug interventionsNot AvailableNot Availableunknown_status
NCT00207857
Test-Retest Reliability of Pulmonary Function Tests in Patients With Duchenne's Muscular DystrophyNo drug interventionsNot AvailableNot Availablewithdrawn
NCT02235844
Allogeneic Human Umbilical Cord Mesenchymal Stem Cells for a Single Male Patient With Duchenne Muscular Dystrophy (DMD)No drug interventionstreatment1completed
NCT05524883
Safety, Tolerability, Pharmacodynamic, Efficacy, and Pharmacokinetic Study of DYNE-251 in Participants With Duchenne Muscular Dystrophy Amenable to Exon 51 Skippingtreatment1 / 2recruiting
NCT01540409
Efficacy, Safety, and Tolerability Rollover Study of Eteplirsen in Subjects With Duchenne Muscular Dystrophytreatment2completed
NCT02814019
A Phase III Double-blind Study With Idebenone in Patients With Duchenne Muscular Dystrophy (DMD) Taking Glucocorticoid Steroidstreatment3terminated
NCT06392724
A Study to Evaluate the Safety and Tolerability of GEN6050X in Duchenne Muscular Dystrophy.No drug interventionstreatment0recruiting
NCT05135663
Extension Study of NS-089/NCNP-02 in DMDNo drug interventionstreatment2active_not_recruiting
NCT01478022
To Compare the Pharmacokinetics Profiles of ISO 20, IBU 200 and IBU Plus ISO Combinations 200 + 20treatment1completed
NCT02614820
The Safety, Efficacy and Tolerability of Remote Ischemic Preconditioning as a Therapy to DMDNo drug interventionstreatmentNot Availableunknown_status
NCT01982695
Cardiomyopathy in DMD: Lisinopril vs. LosartantreatmentNot Availablecompleted
NCT05990608
Peabody Developmental Motor Scaling In Children With Period Duchenne Muscular DystrophyNo drug interventionsNot AvailableNot Availablecompleted
NCT01380964
Research of Biomarkers in Duchenne Muscular Dystrophy PatientsNo drug interventionsNot AvailableNot Availablecompleted
NCT05516745
E-monitoring of PULMonary Function in Patients With Duchenne Muscular Dystrophy at Home"No drug interventionssupportive_careNot Availablerecruiting
NCT02255552
Study of Eteplirsen in DMD Patientstreatment3completed
NCT02036463
A Trial of Chronotherapy of Corticosteroids in Duchenne Muscular Dystrophysupportive_care2withdrawn
NCT04322357
Twice Weekly Steroids and Exercise as Therapy for DMDsupportive_care2recruiting
NCT04184882
A Study to Assess the Safety, Tolerability and Preliminary Efficacy of ASP0367 (MA-0211) in Pediatric Male Participants With Duchenne Muscular Dystrophy (DMD)treatment1terminated
NCT01761292
A Study to Assess Safety/Tolerability, pk, Effects on Histology, Clinical Parameters of Givinostat in Children With DMDtreatment1 / 2completed
NCT04254172
A Low Interventional Study to Monitor Activity Using Wearable Sensors in Duchenne Muscular DystrophyNo drug interventionsNot AvailableNot Availableterminated
NCT00654784
Efficacy and Tolerability of Idebenone in Boys With Cardiac Dysfunction Associated With Duchenne Muscular Dystrophytreatment2completed
NCT02420379
Safety Study of Eteplirsen to Treat Early Stage Duchenne Muscular Dystrophytreatment2completed
NCT02472990
Biomechanical and Morphological Changes in Dystrophic MuscleNo drug interventionsotherNot Availableunknown_status
NCT06100887
Phase 2 Study of EDG-5506 in Children and Adolescents With Duchenne Muscular Dystrophy Previously Treated With Gene Therapy (FOX)treatment2recruiting
NCT00839033
Evaluation of a Mechanical Device During Acute Respiratory Failure in Patients With Neuromuscular DisordersNo drug interventionstreatment3terminated
NCT00592553
Phase 2B Study of PTC124 (Ataluren) in Duchenne/Becker Muscular Dystrophy (DMD/BMD)treatment2completed
NCT02760277
An Extension Study to Assess Vamorolone in Boys With Duchenne Muscular Dystrophy (DMD)treatment2completed
NCT03508947
Safety and Tolerability of WVE-210201 in Patients With Duchenne Muscular Dystrophytreatment1completed
NCT00819845
Ramipril Versus Carvedilol in Duchenne and Becker Patientsprevention4unknown_status
NCT03642145
A Study of Deflazacort (Emflaza®) in Participants With Duchenne Muscular Dystrophy (DMD)treatment3withdrawn
NCT03002298
Virtual Reality in Individuals With Duchenne Muscular DystrophyNo drug interventionstreatmentNot Availablecompleted
NCT02530905
Dose-Titration and Open-label Extension Study of SRP-4045 in Advanced Stage Duchenne Muscular Dystrophy (DMD) Patientstreatment1completed
NCT05641805
Physical Activity Level and Cognitive Functions in Children With Duchenne Muscular DystrophyNo drug interventionsNot AvailableNot Availablerecruiting
NCT02571205
Testosterone Therapy for Pubertal Delay in Duchenne Muscular DystrophyNot AvailableNot Availablecompleted
NCT01963897
Duchenne Muscular Dystrophy < 18y in Norway: Genotype/Phenotype, Growth, Puberty, Bone Health and Quality of Life.No drug interventionsNot AvailableNot Availablecompleted
NCT01126697
Clinical Trial of Coenzyme Q10 and Lisinopril in Muscular Dystrophiestreatment2 / 3completed
NCT06274983
DMD- Interactive Virtual Reality StudyNo drug interventionssupportive_careNot Availableactive_not_recruiting
NCT02667483
Study of DS-5141b in Patients With Duchenne Muscular Dystrophytreatment1 / 2completed
NCT05967793
Effect of Kinesiology Taping on Head and Trunk Control in Children With Duchenne Muscular DystrophyNo drug interventionssupportive_careNot Availablerecruiting
NCT02246478
A Study of TAS-205 for Duchenne Muscular DystrophyNo drug interventionstreatment1completed
NCT00264888
Safety and Efficacy Study of PTC124 in Duchenne Muscular Dystrophytreatment2completed
NCT05849688
Bicycle Training on Ventilatory Functions in Duchenne Muscular DystrophyNo drug interventionstreatmentNot Availablenot_yet_recruiting
NCT04529707
Sleep Intervention in Young Boys With Duchenne Muscular DystrophyNo drug interventionstreatmentNot Availablerecruiting
NCT06280209
A Phase 1/2 Study to Assess the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of BMN 351 in Participants With Duchenne Muscular DystrophyNo drug interventionstreatment1 / 2recruiting
NCT01037309
Phase I/II Study of PRO044 in Duchenne Muscular Dystrophy (DMD)treatment1 / 2completed
NCT04179409
A 48-Week, Open Label, Study to Evaluate the Efficacy and Safety of AMONDYS 45, EXONDYS 51, VYONDYS 53 in Subjects With DuchenneMuscular Dystrophy Carrying Eligible DMD Duplications.treatment2completed
NCT05110885
Public AttitudesTowards SMA and DMD Awareness, Newborn and Carrier Screening and Physiotherapy PracticesNo drug interventionsNot AvailableNot Availableunknown_status
NCT06366815
phenotypeS in Non Ambulant Duchenne Muscular DystrophyNo drug interventionsNot AvailableNot Availablerecruiting
NCT01981915
Optimum Insufflation Capacity in NMDNo drug interventionsdiagnosticNot Availablecompleted
NCT00468832
Longitudinal Study of the Natural History of Duchenne Muscular Dystrophy (DMD)No drug interventionsNot AvailableNot Availableunknown_status
NCT05029232
Comprehensive Study of Duchenne Muscular Dystrophy at Sohag University HospitalNo drug interventionsscreeningNot Availableunknown_status
NCT01422200
Flu Vaccine Study in Neuromuscular Patients 2011prevention4completed
NCT06093100
Wearable Technology to Evaluate Hyperglycemia and HRV in DMD - Longitudinal AimNo drug interventionsNot AvailableNot Availablerecruiting
NCT01957059
A Phase I/II Study of BMN053 in Subjects With Duchenne Muscular Dystrophy (DMD)treatment1 / 2terminated
NCT00606775
The Preventive Efficacy of Carvedilol on Cardiac Dysfunction in Duchenne Muscular Dystrophyprevention4unknown_status
NCT01999075
Stacking Exercises Aid the Decline in FVC and Sick TimeNo drug interventionstreatment4completed
NCT03951675
The Burden of Access in Duchenne Muscular Dystrophy in the USNo drug interventionsNot AvailableNot Availablecompleted
NCT03541070
The Effect of Kinesiology Taping on Balance in Duchenne Muscular DystrophyNo drug interventionssupportive_careNot Availablecompleted
NCT04335942
Characterization of the Postural Habits of Wheelchair Users Analysis of the Acceptability of International Recommendations in the Prevention of Pressure Sores Risk by Using a Connected Textile SensorNo drug interventionspreventionNot Availablecompleted
NCT06402942
Gamified Occupational Therapy for Adolescents With Duchenne Muscular DystrophyNo drug interventionssupportive_careNot Availablerecruiting
NCT05693142
AFFINITY DUCHENNE: RGX-202 Gene Therapy in Participants With Duchenne Muscular Dystrophy (DMD)treatment1 / 2recruiting
NCT03532542
An Extension Study to Evaluate Casimersen or Golodirsen in Patients With Duchenne Muscular Dystrophytreatment3terminated
NCT05549999
Cultural Adaptation, Validity, and Reliability of the Turkish Version of North Star Ambulatory AssessmentNo drug interventionsNot AvailableNot Availablecompleted
NCT04060199
Study to Assess the Efficacy and Safety of Viltolarsen in Ambulant Boys With DMD (RACER53)treatment3completed
NCT03038399
Long-term Extension Study to Assess Vamorolone in Boys With Duchenne Muscular Dystrophy (DMD)treatment2completed
NCT05338099
Determine the Safety and Dose of EN001 in Patients With Duchenne Muscular Dystrophy(DMD)No drug interventionstreatment1completed
NCT06379906
Upper Extremity Muscle Strength, Balance and Functional Skills in DMDNo drug interventionsNot AvailableNot Availablecompleted
NCT06103006
Remote Physiotherapy to Protect Physical Health in Duchenne Muscular DystrophyNo drug interventionstreatmentNot Availablecompleted
NCT02310906
Phase I/II Study of SRP-4053 in DMD Patientstreatment1 / 2completed
NCT03534349
Lower Limb Flexibility in Duchenne Muscular Dystrophy: Effects on Functional PerformanceNo drug interventionsNot AvailableNot Availablecompleted
NCT06079736
A Study Of PGN-EDO51 In Participants With Duchenne Muscular Dystrophy Amenable To Exon 51-Skipping TreatmentNo drug interventionstreatment2recruiting
NCT03786913
Quantitative Muscle Ultrasound as a Marker of Progression in Children With Muscular DiseasesNo drug interventionsNot AvailableNot Availablecompleted
NCT02907619
An Open-label Extension Study To Evaluate Safety Of PF-06252616 In Boys With Duchenne Muscular Dystrophytreatment2terminated
NCT05982119
Assessments in Patients With Muscular Pathology and in Control Subjects : The ActiLiège Next StudyNo drug interventionsbasic_scienceNot Availablerecruiting
NCT02592941
Deflazacort Expanded Access Program for Children, Adolescents and Adults With Duchenne Muscular DystrophyNot AvailableNot Availableapproved_for_marketing
NCT02167217
Historically Controlled Trial of Corticosteroids in Young Boys With Duchenne Muscular Dystrophytreatment2completed
NCT01385917
Observational Study of Patients With Duchenne Muscular Dystrophy Theoretically Treatable With Exon 53 SkippingNo drug interventionsNot AvailableNot Availableunknown_status
NCT04173234
Aerobic Exercise in Duchenne Muscular DystrophyNo drug interventionstreatmentNot Availablecompleted
NCT02891434
Analysis of a Virtual Reality Task in Patients With Duchenne Muscular DystrophyNo drug interventionssupportive_careNot Availablecompleted
NCT02241434
Stem Cell Therapy in Duchenne Muscular DystrophyNo drug interventionstreatment1withdrawn
NCT02376816
Clinical Intramuscular Gene Transfer Trial of rAAVrh74.MCK.Micro-Dystrophin to Patients With Duchenne Muscular DystrophyNo drug interventionstreatment1completed
NCT03354039
Tamoxifen in Duchenne Muscular Dystrophytreatment3completed
NCT06450639
An Open-label Study to Assess the Efficacy and Safety of Satralizumab in Duchenne Muscular Dystrophytreatment2not_yet_recruiting
NCT01396239
Efficacy Study of AVI-4658 to Induce Dystrophin Expression in Selected Duchenne Muscular Dystrophy Patientstreatment2completed
NCT05185622
A Study to Assess Vamorolone in Boys Ages 2 to <4 Years and 7 to <18 Years With Duchenne Muscular Dystrophy (DMD)treatment2active_not_recruiting
NCT02081625
Exploratory Study of NS-065/NCNP-01 in DMDtreatment1completed
NCT06174025
Validity and Reliability of the 6 Minute Pegboard Ring TestNo drug interventionsNot AvailableNot Availablecompleted
NCT05670730
Study of AOC 1044 in Healthy Adult Volunteers and Participants With Duchenne Muscular Dystrophy (DMD) Mutations Amenable to Exon 44 SkippingNo drug interventionstreatment1 / 2recruiting
NCT02994030
Biomarker for Duchenne Muscular DystrophyNo drug interventionsNot AvailableNot Availablecompleted
NCT05575648
Dual Task in Duchenne Muscular DystrophyNo drug interventionsdiagnosticNot Availablecompleted
NCT05933057
Efficacy, Safety and Tolerability of Givinostat in Non-ambulant Patients With Duchenne Muscular Dystrophytreatment3recruiting
NCT02819557
Study of Ataluren in ≥2 to <5 Year-Old Male Participants With Duchenne Muscular Dystrophytreatment2completed
NCT01633866
Pediatric Radio Frequency Coils GenericNo drug interventionsNot AvailableNot Availableactive_not_recruiting
NCT04004065
Two-Part Study for Dose Determination of Vesleteplirsen (SRP-5051) (Part A), Then Dose Efficacy (Part B) in Participants With Duchenne Muscular Dystrophy Amenable to Exon 51-Skipping Treatmenttreatment2active_not_recruiting
NCT01826474
Phase IIb Study of PRO045 in Subjects With Duchenne Muscular Dystrophytreatment1 / 2terminated
NCT00005574
Gentamicin Treatment of Muscular Dystrophytreatment1completed
NCT06564974
Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy.Not AvailableNot Availablerecruiting
NCT04687020
Long-term Use of Viltolarsen in Boys With Duchenne Muscular Dystrophy in Clinical Practice (VILT-502)treatment4active_not_recruiting
NCT04287582
The Evaluation of Muscle Activation in Climbing up Stairs Activity in Children With Duchenne Muscular DystrophyNo drug interventionsNot AvailableNot Availableunknown_status
NCT01847573
Safety, Tolerability, and Pharmacokinetics of Single and Multiple Doses of HT-100 in Duchenne Muscular Dystrophytreatment1 / 2terminated
NCT03589573
Effect of Muscle Strength on Hamstring Flexibility in Children With Duchenne Muscular DystrophyNo drug interventionsNot AvailableNot Availablecompleted
NCT02285673
Efficacy of Umbilical Cord Mesenchymal Stem Cells in Duchenne Muscular DystrophyNo drug interventionstreatment1 / 2unknown_status
NCT06491927
Long Term Follow-up for RGX-202No drug interventionsNot AvailableNot Availableenrolling_by_invitation
NCT03648827
A Study to Assess Dystrophin Levels in Participants With Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD)treatment2completed
NCT00759876
Phase 2a Extension Study of Ataluren (PTC124) in Duchenne Muscular Dystrophy (DMD)treatment2terminated
NCT04428476
Open-label Extension of the HOPE-2 Trialtreatment2active_not_recruiting
NCT02484560
Efficacy of Stem Cell Therapy in Ambulatory and Non-ambulatory Children With Duchenne Muscular Dystrophy - Phase 1-2No drug interventionstreatment1unknown_status
NCT03689660
Feasibility of Virtual Reality in Children With Neuromuscular Disease, Effectiveness of Virtual Reality and BiofeedbackNo drug interventionstreatmentNot Availableunknown_status
NCT01009294
Study of Ataluren (PTC124) in Nonambulatory Participants With Nonsense-Mutation-Mediated Duchenne/Becker Muscular Dystrophy (nmDMD/BMD)treatment2terminated
NCT03936894
Single Escalating Dose Pilot Trial of Canakinumab (ILARIS®) in Duchenne Muscular Dystrophytreatment1 / 2active_not_recruiting
NCT05564962
Quality and Independence of Gait Classification Scale for DMD (QIGS-DMD)No drug interventionsNot AvailableNot Availablecompleted
NCT01081080
Cardiac Magnetic Resonance in Children With Muscular DystrophyNo drug interventionsNot AvailableNot Availablecompleted
NCT02972580
Characterization of Clinical Skeletal and Cardiac Impairment in Carriers of DMD and BMDNo drug interventionsNot AvailableNot Availableactive_not_recruiting
NCT03760029
A Natural History Study In Chinese Male Patients With Duchenne Muscular DystrophyNo drug interventionsotherNot Availablecompleted
NCT04956289
Study to Assess the Safety, Tolerability, and Efficacy of Viltolarsen in Ambulant and Non-Ambulant Boys With DMD (Galactic53)treatment2completed
NCT02780492
Outcome Measures in Duchenne Muscular Dystrophy: A Natural History StudyNo drug interventionsNot AvailableNot Availablecompleted
NCT03529240
Kinesiology Taping in Duchenne Muscular Dystrophy: Effects on Performance, Gait Characteristics, and Energy ConsumptionNo drug interventionssupportive_careNot Availablecompleted
NCT04632940
Phase 3 Trial of Pamrevlumab or Placebo in Combination With Systemic Corticosteroids in Participants With Ambulatory DMDtreatment3terminated
NCT01610440
Safety and Efficacy of Umbilical Cord Mesenchymal Stem Cell Therapy for Patients With Duchenne Muscular Dystrophytreatment1 / 2unknown_status
NCT01183767
Sunphenon Epigallocatechin-Gallate (EGCg) in Duchenne Muscular Dystrophytreatment2 / 3completed
NCT02196467
Transplantation of Myoblasts to Duchenne Muscular Dystrophy (DMD) PatientsNo drug interventionstreatment1 / 2unknown_status
NCT01580501
PDE Inhibitors in DMD Study (Acute Dosing Study)treatment1completed
NCT01540604
CRD007 for the Treatment of Duchenne Muscular Dystrophy, Becker Muscular Dystrophy and Symptomatic CarriersNo drug interventionsNot Available2completed
NCT04972604
CureDuchenne Link®: A Resource for ResearchNo drug interventionsNot AvailableNot Availablerecruiting
NCT04120168
Study Determining the Frequency of Duchenne Muscular Dystrophy and Late-onset Pompe DiseaseNo drug interventionsNot AvailableNot Availablecompleted
NCT00110669
High-dose Prednisone in Duchenne Muscular Dystrophytreatment3completed
NCT02329769
Open Label, Extension Study of PRO044 in Duchenne Muscular Dystrophy (DMD)treatment2terminated
NCT06539169
FLOWER: Following Longitudinal Outcomes With Epidemiology for Rare DiseasesNo drug interventionsNot AvailableNot Availablerecruiting
NCT01521546
Eplerenone for Subclinical Cardiomyopathy in Duchenne Muscular DystrophytreatmentNot Availablecompleted
NCT00004646
Phase III Randomized, Double-Blind Study of Prednisone for Duchenne Muscular Dystrophytreatment3completed
NCT05464446
Examination of Lower Urinary System Symptoms With Duchenne Muscular DystrophyNo drug interventionsNot AvailableNot Availablecompleted
NCT03589612
Regression of Hamstring Flexibility and Performance in Children With Duchenne Muscular DystrophyNo drug interventionsNot AvailableNot Availablecompleted
NCT05436210
Postural and Anthropometric Properties of Foot and Ankle of Patients With DMDNo drug interventionsNot AvailableNot Availablecompleted
NCT02500381
Study of SRP-4045 (Casimersen) and SRP-4053 (Golodirsen) in Participants With Duchenne Muscular Dystrophy (DMD)treatment3active_not_recruiting
NCT05244395
Development of a New Instrument to Evaluate Gait Characteristics of Individuals With Duchenne Muscular DystrophyNo drug interventionsotherNot Availablecompleted
NCT03218995
Study of Eteplirsen in Young Participants With Duchenne Muscular Dystrophy (DMD) Amenable to Exon 51 Skippingtreatment2completed
NCT04240314
AAV9 U7snRNA Gene Therapy to Treat Boys With DMD Exon 2 Duplications.treatment1 / 2active_not_recruiting
NCT02168114
Magnetic Resonance and Optical Imaging of Dystrophic and Damaged MuscleNo drug interventionsdiagnosticNot Availablecompleted
NCT03372655
Prognostic Factors Affecting Duchenne Muscular DystrophyNo drug interventionsNot AvailableNot Availableunknown_status
NCT01066455
Cardiac Outcome Measures in Children With Muscular DystrophyNo drug interventionsNot AvailableNot Availablecompleted
NCT05274555
Reliability and Validity of the Turkish Version of the Upper Limb Short Questionnaire in Duchenne Muscular DystrophyNo drug interventionsNot AvailableNot Availablecompleted
NCT01491555
Electrical Impedance Myography and Ultrasound as Biomarkers of Duchenne Muscular DystrophyNo drug interventionsNot AvailableNot Availablecompleted
NCT00159250
Safety and Efficacy Study of Antisense Oligonucleotides in Duchenne Muscular Dystrophytreatment1 / 2completed
NCT05938023
A Study of ATL1102 or Placebo in Participants With Non-ambulatory Duchenne Muscular Dystrophytreatment2active_not_recruiting
NCT03655223
Early Check: Expanded Screening in NewbornsNo drug interventionsNot AvailableNot Availableenrolling_by_invitation
NCT01168908
Revatio for Heart Disease in Duchenne Muscular Dystrophy and Becker Muscular Dystrophytreatment2terminated
NCT05016908
Extracellular RNA Biomarkers of Duchenne Muscular DystrophyNo drug interventionsNot AvailableNot Availablerecruiting
NCT01207908
Safety and Efficacy Study of IGF-1 in Duchenne Muscular Dystrophytreatment1 / 2completed
NCT06565208
First in Human SAD/MAD Safety and PK Study With Adult DMD Safety and PK CohortNo drug interventionstreatment0recruiting
NCT02418338
2D Strain Evaluation: Children With Duchenne Muscular Dystrophy Versus Healthy ChildrenNo drug interventionsdiagnosticNot Availablecompleted
NCT05657938
Evaluation of Home Based Assessments on Participants With DMDNo drug interventionsNot AvailableNot Availablecompleted
NCT02485938
HOPE-Duchenne (Halt cardiomyOPathy progrEssion in Duchenne)treatment1 / 2completed
NCT01772043
Duchenne Muscular Dystrophy Tissue Bank for Exon SkippingNo drug interventionsNot AvailableNot Availableunknown_status
NCT05996003
NS-089/NCNP-02-201 in Boys With Duchenne Muscular Dystrophy (DMD)treatment2recruiting
NCT03333590
Gene Transfer Clinical Trial to Deliver rAAVrh74.MCK.GALGT2 for Duchenne Muscular Dystrophytreatment1 / 2active_not_recruiting
NCT02760264
A Study to Assess Vamorolone in Boys With Duchenne Muscular Dystrophy (DMD)treatment2completed
NCT05689164
A Study to Understand the Long-term Safety and Effects of an Experimental Gene Therapy for Duchenne Muscular Dystrophy.other3recruiting
NCT06128564
A Gene Delivery Study to Evaluate the Safety and Expression of Delandistrogene Moxeparvovec in Participants Under the Age of Four With Duchenne Muscular Dystrophy (DMD)No drug interventionstreatment2recruiting
NCT05096221
A Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD)No drug interventionstreatment3active_not_recruiting
NCT02958202
Extension Study of BMN 044 in Duchenne Muscular Dystrophy (DMD)treatment2terminated
NCT03362502
A Study to Evaluate the Safety and Tolerability of PF-06939926 Gene Therapy in Duchenne Muscular Dystrophytreatment1active_not_recruiting
NCT04384354
Digestive Events in Duchenne Muscular Dystrophy PatientsNo drug interventionsNot AvailableNot Availablecompleted
NCT04740554
Heart Rate Variability in Individuals With Duchenne Muscular DystrophyNo drug interventionsNot AvailableNot Availablecompleted
NCT05967351
A Long-term Follow-up Study of Participants Who Received Delandistrogene Moxeparvovec (SRP-9001) in a Previous Clinical StudyNo drug interventionsother3enrolling_by_invitation
NCT02964377
Plus Epicatechin Duchenne Muscular Dystrophy in Non-ambulatory Adolescentstreatment1 / 2completed
NCT00312247
Biomechanical Analysis of Gait in Individuals With Duchenne Muscular DystrophyNo drug interventionsNot AvailableNot Availablecompleted
NCT05712447
Duchenne Muscular Dystrophy Video Assessment RegistryNo drug interventionsNot AvailableNot Availablerecruiting
NCT01645098
Sedation During Muscle Biopsy in Patients With Duchenne Muscular DystrophytreatmentNot Availablecompleted
NCT02034305
Peak Cough Flow and Cough Clearance in Patients With Muscular DystrophyNo drug interventionsNot AvailableNot Availablecompleted
NCT00844597
Dose-Ranging Study of AVI-4658 to Induce Dystrophin Expression in Selected Duchenne Muscular Dystrophy (DMD) Patientstreatment1 / 2completed
NCT02851797
Clinical Study to Evaluate the Efficacy and Safety of Givinostat in Ambulant Patients With Duchenne Muscular Dystrophytreatment3completed
NCT05249361
Correlation Between Functional Capacity and Functional Capability in Duchenne Muscular DystrophyNo drug interventionsNot AvailableNot Availablerecruiting
NCT01099761
Study of ACE-031 in Subjects With Duchenne Muscular Dystrophytreatment2terminated
NCT06412328
Psychoeducation Program for Parents of Children With DMDNo drug interventionssupportive_careNot Availablecompleted
NCT03521271
Investigation Of Factors Affecting Hand Functions in Nonambulatory Patients With Duchenne Muscular DystrophyNo drug interventionsNot AvailableNot Availablecompleted
NCT05661071
Neuropsychological Profiles of Children With Duchenne Muscular Dystrophy and Its Effects on Motor FunctionsNo drug interventionsNot AvailableNot Availableactive_not_recruiting
NCT06054971
NSAA NON-Interventional Study ProtocolNo drug interventionsNot AvailableNot Availablerecruiting
NCT04012671
A Registered Cohort Study on Duchenne Muscular DystrophyNo drug interventionsNot AvailableNot Availablerecruiting
NCT01484678
Magnetic Resonance Imaging and Biomarkers for Muscular DystrophyNo drug interventionsNot AvailableNot Availablerecruiting
NCT03985878
A Study to Evaluate Safety, Tolerability, and Efficacy of Eteplirsen in Participants With Duchenne Muscular Dystrophy (DMD) Who Have Completed Study 4658-102 (NCT03218995)treatment2terminated
NCT03603288
Phase III Study With Idebenone in Patients With Duchenne Muscular Dystrophy (SIDEROS-E)treatment3terminated
NCT03531788
Use of Dynamic Arm Supports to Promote Activities of Daily Living in Individuals With DMDNo drug interventionstreatmentNot Availableterminated
NCT01603407
Finding the Optimum Regimen for Duchenne Muscular Dystrophytreatment3completed
NCT03433807
Expanded Access Program for Idebenone in Participants With Duchenne Muscular Dystrophy (DMD)Not AvailableNot Availableno_longer_available
NCT01247207
Study of Ataluren in Previously Treated Participants With Nonsense Mutation Dystrophinopathy (nmDBMD)treatment3enrolling_by_invitation
NCT01125709
Comparative Study of Clinical Endpoint in DMD: Handheld Myometry (HHM) Versus CINRG Quantitative Measurement System (CQMS)No drug interventionsNot AvailableNot Availablecompleted
NCT02069756
The Duchenne RegistryNo drug interventionsNot AvailableNot Availablerecruiting
NCT06114056
A Clinical Study Evaluating the Safety, Tolerability, and Initial Efficacy of Single Intravenous Infusion of JWK007 in Patients With Duchenne Muscular Dystrophy (DMD)No drug interventionstreatment1recruiting
NCT04281485
Study to Evaluate the Safety and Efficacy of PF-06939926 for the Treatment of Duchenne Muscular DystrophyNo drug interventionstreatment3active_not_recruiting
NCT02516085
Improved Muscle Function in Duchenne Muscular Dystrophy Through L-Arginine and Metformintreatment1completed
NCT06445985
Hydrotherapy in Duchenne Muscular Dystrophy (DMD)No drug interventionssupportive_careNot Availablerecruiting
NCT04193085
Wearable Technology to Assess Gait Function in SMA and DMDNo drug interventionsNot AvailableNot Availablecompleted
NCT03443115
Duchenne Muscular Dystrophy Heart StudyNo drug interventionsNot AvailableNot Availableunknown_status
NCT03796637
A Study to Assess Dystrophin Levels in Participants With Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD) Who Have Been Treated With Atalurenother2completed
NCT06579352
Expanded Access Study of UC-MSC in DMD PatientsNot AvailableNot Availableavailable
NCT02354352
Therapeutic Potential for Aldosterone Inhibition in Duchenne Muscular Dystrophytreatment3completed
NCT02251600
A Pharmacokinetic Study of Oral Deflazacort in Children and Adolescent Subjects With Duchenne Muscular Dystrophybasic_science1completed
NCT03836300
Parent and Infant Inter(X)Action Intervention (PIXI)No drug interventionstreatmentNot Availableenrolling_by_invitation
NCT01557400
Study of Ataluren for Previously Treated Participants With Nonsense Mutation Duchenne/Becker Muscular Dystrophy (nmDBMD) in Europe, Israel, Australia, and Canadatreatment3completed
NCT06579859
Development of a Registry to Assess Natural History in Duchenne Muscular DystrophyNo drug interventionsNot AvailableNot Availablenot_yet_recruiting
NCT01874275
Duchenne Muscular Dystrophy Clinical TrialNo drug interventionstreatmentNot Availablecompleted
NCT05195775
Tadalafil as Adjuvant Therapy for DMDtreatment2 / 3recruiting
NCT03439670
A Study to Assess the Efficacy and Safety of Vamorolone in Boys With Duchenne Muscular Dystrophy (DMD)treatment2completed
NCT01359670
Tadalafil and Sildenafil for Duchenne Muscular Dystrophytreatment0completed
NCT03368742
Microdystrophin Gene Transfer Study in Adolescents and Children With DMDNo drug interventionstreatment1 / 2active_not_recruiting
NCT05514249
Treatment of a Single Patient With CRD-TMH-001No drug interventionstreatment1unknown_status
NCT02606136
Trial of Pamrevlumab (FG-3019), in Non-Ambulatory Participants With Duchenne Muscular Dystrophy (DMD)treatment2terminated
NCT05558813
Natural History of Duchenne Muscular Dystrophy Cardiomyopathy (DMD-CMP)No drug interventionsdiagnosticNot Availablenot_yet_recruiting
NCT00308113
CoQ10 and Prednisone in Non-Ambulatory DMDtreatment3terminated
NCT06295718
Tele-assessment of Functional Performance and Quality of Life in Patients With Duchenne Muscular Dystrophy: Validity and Reliability StudyNo drug interventionsNot AvailableNot Availableenrolling_by_invitation
NCT03863119
Expanded Access Protocol for Boys With Duchenne Muscular DystrophyNot AvailableNot Availableavailable
NCT06270719
An Observational Study Comparing Delandistrogene Moxeparvovec With Standard of Care in Participants With Duchenne Muscular DystrophyNo drug interventionsNot AvailableNot Availablerecruiting
NCT03917719
An Open-Label Extension Study of Edasalonexent in Boys With Duchenne Muscular Dystrophytreatment3terminated
NCT04583917
Brain Involvement in Dystrophinopathies Part 1No drug interventionsNot AvailableNot Availablecompleted
NCT04433234
Long-term, Extension Study of DS-5141b in Patients With Duchenne Muscular Dystrophytreatment2active_not_recruiting
NCT01648634
Nebivolol for the Prevention of Left Ventricular Systolic Dysfunction in Patients With Duchenne Muscular Dystrophyprevention3completed
NCT04607824
Heart Rate Variability in Duchenne Muscular Dystrophy During Computer TaskNo drug interventionsNot AvailableNot Availablecompleted
NCT01182324
The PTC124 (Ataluren) Clinical Trial for Duchenne Muscular Dystrophy: Exploration of the Experiences of Parents, Clinician Researchers, and the Industry SponsorNo drug interventionsNot AvailableNot Availablecompleted
NCT04668716
Brain Involvement in Dystrophinopathies Part 2No drug interventionsNot AvailableNot Availablecompleted
NCT06124196
Wearable Technology to Evaluate Hyperglycemia and HRV in DMDNo drug interventionsNot AvailableNot Availablerecruiting
NCT01239758
Extension Study of ACE-031 in Subjects With Duchenne Muscular Dystrophytreatment2terminated
NCT03558958
Safety and Efficacy of P-188 NF in DMD PatientsNo drug interventionstreatment2terminated
NCT00428935
Safety Study of Mini-dystrophin Gene to Treat Duchenne Muscular DystrophyNo drug interventionstreatment1completed
NCT02310763
A Phase 2 Study to Evaluate the Safety, Efficacy, Pharmacokinetics and Pharmacodynamics of PF-06252616 in Duchenne Muscular Dystrophytreatment2terminated
NCT05601986
Motor Imagery on Children With DMD on Gait and Balance FunctionsNo drug interventionssupportive_careNot Availablerecruiting
NCT02636686
Extension Study of Drisapersen in DMD SubjectsNot AvailableNot Availableno_longer_available
NCT03039686
Clinical Trial to Evaluate the Efficacy, Safety, and Tolerability of RO7239361 in Ambulatory Boys With Duchenne Muscular Dystrophytreatment2 / 3completed
NCT06138639
A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)No drug interventionstreatment1 / 2recruiting
NCT05019625
Biomarker Development for Muscular DystrophiesNo drug interventionsNot AvailableNot Availablerecruiting
NCT06328725
Evaluate the Efficacy and Safety of EN001 in Patients With Duchenne Muscular Dystrophytreatment1 / 2not_yet_recruiting
NCT00758225
Long-term Safety, Tolerability and Efficacy of Idebenone in Duchenne Muscular Dystrophy (DELPHI Extension)treatment2completed
NCT02704325
Gene Transfer Clinical Trial for Duchenne Muscular Dystrophy Using rAAVrh74.MCK.GALGT2treatment1 / 2withdrawn
NCT05280730
Assessment of Neurodevelopmental Needs in Duchenne Muscular DystrophyNo drug interventionsNot AvailableNot Availablerecruiting
NCT03319030
Aerobic Exercise in Boys With Duchenne Muscular Dystrophy (DMD)No drug interventionsNot AvailableNot Availablecompleted
NCT02752048
A Phase IIa Study of TAS-205 for Duchenne Muscular DystrophyNo drug interventionstreatment2completed
NCT02295748
An Open-Label, Long-Term Extension Study to Evaluate the Safety and Tolerability Deflazacorttreatment1completed
NCT04371666
Phase 3 Trial of Pamrevlumab or Placebo With Systemic Corticosteroids in Participants With Non-ambulatory Duchenne Muscular Dystrophy (DMD)treatment3terminated
NCT01978366
Open Label Extension Study of HT-100 in Patients With DMDtreatment2terminated
NCT03680365
Your Voice; Impact of Duchenne Muscular Dystrophy (DMD) on the Lives of FamiliesNo drug interventionsNot AvailableNot Availablecompleted
NCT06540365
Applying the Pathways and Resources for Engagement and Participation Protocol Among People With Muscles DystrophiesNo drug interventionstreatmentNot Availablenot_yet_recruiting
NCT00451074
Six Month Study of Gentamicin in Duchenne Muscular Dystrophy With Stop Codonstreatment1completed
NCT03552874
Pulmonary and Upper Limb Functions in Duchenne Muscular DystrophyNo drug interventionsNot AvailableNot Availablecompleted
NCT02436720
Upper Limb Assessment in Duchenne Muscular DystrophyNo drug interventionsNot AvailableNot Availableunknown_status
NCT05281120
Effects of Low-level Mechanical Vibration on Bone Density in Ambulant Children Affected by Duchenne Muscular DystrophyNo drug interventionstreatmentNot Availablecompleted
NCT03067831
Bone Marrow-Derived Autologous Stem Cells for the Treatment of Duchenne Muscular DystrophyNo drug interventionstreatment1 / 2unknown_status
NCT03882827
Natural History of Duchenne Muscular DystrophyNo drug interventionsNot AvailableNot Availableunknown_status
NCT05305976
Telerehabilitation in Duchenne Muscular DystrophyNo drug interventionspreventionNot Availablecompleted
NCT04906460
Open-label Study of WVE-N531 in Patients With Duchenne Muscular Dystrophy (FORWARD-53)treatment1 / 2active_not_recruiting
NCT05540860
A Study of EDG-5506 in Children With Duchenne Muscular Dystrophy (LYNX)treatment2recruiting
NCT05412394
Once Weekly Infant Corticosteroid Trial for DMDtreatment4recruiting
NCT04129294
Exploratory Study of NS-089/NCNP-02 in DMDNo drug interventionstreatment1 / 2completed
NCT04768062
Study to Assess the Safety and Efficacy of Viltolarsen in Ambulant Boys With DMD (RACER53-X)treatment3active_not_recruiting
NCT02858362
Proof of Concept Study to Assess Activity and Safety of SMT C1100 (Ezutromid) in Boys With Duchenne Muscular Dystrophy (DMD)treatment2terminated
NCT05753462
Phase 1/2a for Safety, PK and PD of SQY51 in Paediatric and Adult Patients Duchenne Muscular DystrophyNo drug interventionsother1 / 2recruiting
NCT03611244
Prevention of Scoliosis in Patients With Duchenne Muscular Dystrophy Using Portable Seat DeviceNo drug interventionspreventionNot Availablerecruiting
NCT01931644
At-Home Research Study for Patients With Autoimmune, Inflammatory, Genetic, Hematological, Infectious, Neurological, CNS, Oncological, Respiratory, Metabolic ConditionsNo drug interventionsNot AvailableNot Availablecompleted
NCT01954940
Whole Body Vibration Therapy in Boys With Duchenne Muscular DystrophyNo drug interventionspreventionNot Availablecompleted
NCT04782440
The Effect of Telerehabilitation of Patients With Duchenne Muscular DystrophyNo drug interventionssupportive_careNot Availableunknown_status
NCT03513367
The Validation Process for Confirmation of the French Version of the Pediatric Quality of Life Inventory :PedsQLTM.No drug interventionsNot AvailableNot Availableunknown_status
NCT01753804
A Prospective Natural History Study of Progression of Subjects With Duchenne Muscular Dystrophy.No drug interventionsNot AvailableNot Availableterminated
NCT03907072
Efficacy and Safety Study of WVE-210201 (Suvodirsen) With Open-label Extension in Ambulatory Patients With Duchenne Muscular Dystrophytreatment2 / 3terminated
NCT02740972
Safety and Dose Finding Study of NS-065/NCNP-01 in Boys With Duchenne Muscular Dystrophy (DMD)treatment2completed
NCT03373968
Givinostat in Duchenne's Muscular Dystrophy Long-term Safety and Tolerability Studytreatment2 / 3enrolling_by_invitation
NCT03779646
Bisoprolol in DMD Early Cardiomyopathytreatment2 / 3unknown_status
NCT03947112
Physical Activity Level of Norwegian Boys With Duchenne Muscular DystrophyNo drug interventionsNot AvailableNot Availablecompleted
NCT05559710
Motor Imagery in Duchenne Muscular DystrophyNo drug interventionsNot AvailableNot Availablecompleted
NCT02354781
Clinical Intramuscular Gene Transfer of rAAV1.CMV.huFollistatin344 Trial to Patients With Duchenne Muscular Dystrophyother1 / 2completed
NCT01335295
Safety Study of Flavocoxid in Duchenne Muscular DystrophyNo drug interventionsNot Available1completed
NCT05330195
Bicycle Ergometer Training in Duchenne Muscular DystrophyNo drug interventionstreatmentNot Availablecompleted
NCT04708314
An Open-Label Study of Golodirsen in Non-Ambulant Patients With Duchenne Muscular Dystrophytreatment4terminated
NCT06053814
NS-050/NCNP-03 in Boys With DMD (Meteor50)No drug interventionstreatment1 / 2not_yet_recruiting
NCT03167255
Extension Study of NS-065/NCNP-01 in Boys With Duchenne Muscular Dystrophy (DMD)treatment2completed
NCT06241950
A Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of Delandistrogene Moxeparvovec (SRP-9001) Following Imlifidase Infusion in Participants With Duchenne Muscular Dystrophy (DMD) Determined to Have Pre-existing Antibodies to Recombinant Adeno-Associated Virus Serotype (rAAVrh74)treatment1enrolling_by_invitation
NCT02421523
Strength Training in Duchenne Muscular DystrophyNo drug interventionshealth_services_researchNot Availablecompleted
NCT02340923
A Device for Rapid, Painless, Bedside Muscle Evaluation of ChildrenNo drug interventionsNot AvailableNot Availablecompleted
NCT02056808
A Phase 1b Study of SMT C1100 in Subjects With Duchenne Muscular Dystrophy (DMD)treatment1completed
NCT05881408
A Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of Delandistrogene Moxeparvovec (SRP-9001) in Non-Ambulatory and Ambulatory Participants With Duchenne Muscular Dystrophy (DMD)No drug interventionstreatment3recruiting
NCT04587908
A Phase 3 Study of TAS-205 in Patients With Duchenne Muscular Dystrophy(REACH-DMD)No drug interventionstreatment3active_not_recruiting
NCT01098708
This is a Study to Get More Information About Non Ambulatory Boys & Men With Duchenne Muscular DystrophyNo drug interventionsNot AvailableNot Availablecompleted
NCT06109103
Telerehabilitation-based Motor Imagery Training in Children With Duchenne Muscular DystrophyNo drug interventionstreatmentNot Availablenot_yet_recruiting
NCT03375164
A Gene Transfer Therapy Study to Evaluate the Safety of Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD)No drug interventionstreatment1 / 2completed
NCT06304064
Halt cardiomyOPathy progrEssion in Duchenne (HOPE-OLE)treatment2completed
NCT01523964
DART Electrical Impedance Myography (EIM) Trial in Duchenne Muscular Dystrophy (DMD) and Healthy ControlsNo drug interventionsNot AvailableNot Availablecompleted
NCT01388764
Safety, Tolerability and Effects of L-Arginine in Boys With Dystrophinopathy on CorticosteroidsNot Available1completed
NCT02525302
HT-100 Long-term Study in DMD Patients Who Completed HALO-DMD-02treatment2terminated
NCT03057002
UTSW HP [13-C] Pyruvate Injection in HCMNo drug interventionsNot AvailableNot Availablerecruiting
NCT03335384
Relationship Between PFTs and Pdi in DMDNo drug interventionshealth_services_researchNot Availablewithdrawn
NCT00847379
Phase 2B Extension Study of Ataluren (PTC124) in Duchenne/Becker Muscular Dystrophy (DMD/BMD)treatment2terminated
NCT02835079
Treatment Effect of Tamoxifen on Patients With DMDtreatment1completed
NCT05683379
AFFINITY BEYOND: Anti-AAV8 Antibody Assessment Study of Boys With DMDNo drug interventionsNot AvailableNot Availablerecruiting
NCT01995032
L-citrulline and Metformin in Duchenne's Muscular Dystrophytreatment3completed
NCT05209087
Effects of Parental Influence on Physical Activity Level and Participation in Children With Duchenne Muscular DystrophyNo drug interventionsNot AvailableNot Availablecompleted
NCT03963453
Regular Physical Exercise in Duchenne Muscular DystrophyNo drug interventionsNot AvailableNot Availablecompleted
NCT00102453
Pentoxifylline in Duchenne Muscular Dystrophytreatment1 / 2completed
NCT04669847
The Effects of Trunk Exercises on Upper Extremity and Respiratory Functions in DMDNo drug interventionstreatmentNot Availablecompleted
NCT00033813
KUL0401: An Open-label Pilot Study of Oxatomide in Steroid-Naive Duchenne Muscular Dystrophytreatment2completed
NCT01506518
Double Push Acoustic Radiation Force (DP ARF) Ultrasound for Monitoring Degeneration in Duchenne Muscular DystrophyNo drug interventionsNot AvailableNot Availablecompleted
NCT03777319
Spironolactone Versus Prednisolone in DMDtreatment1terminated
NCT03789734
Safety Study of BLS-M22 in Healthy Volunteerstreatment1completed
NCT01826422
Effect of EPA and DHA in the Inflammation and Metabolic Disorders in DMD/DMB PatientsNo drug interventionspreventionNot Availablecompleted
NCT03992430
A Study to Compare Safety and Efficacy of a High Dose of Eteplirsen in Participants With Duchenne Muscular Dystrophy (DMD) (MIS51ON)treatment3active_not_recruiting
NCT03675126
An Open-Label Extension Study for Patients With Duchenne Muscular Dystrophy Who Participated in Studies of SRP-5051 (Vesleteplirsen)treatment1 / 2terminated
NCT04626674
A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD)No drug interventionstreatment1active_not_recruiting
NCT03703882
Phase III Study of Edasalonexent in Boys With Duchenne Muscular Dystrophytreatment3completed
NCT02710591
Rimeporide in Patients With Duchenne Muscular Dystrophytreatment1completed
NCT05429372
Study of Fordadistrogene Movaparvovec in Early Stage Duchenne Muscular DystrophyNo drug interventionstreatment2active_not_recruiting
NCT06147414
Development of Non-Invasive Prenatal Diagnosis for Single Gene DisordersNo drug interventionsNot AvailableNot Availablenot_yet_recruiting
NCT03375255
A Study to Evaluate the Safety, Tolerability, and Pharmacokinetics of a Single Dose of SRP-5051 (Vesleteplirsen) in Patients With Duchenne Muscular Dystrophy (DMD)treatment1completed
NCT00296621
Effect of Oral Glutamine on Muscle Mass and Function in Duchenne Muscular Dystrophytreatment2completed
NCT05066633
The Efficacy and Safety of Metoprolol as add-on Treatment to Standard of Care in Preventing Cardiomyopathy in Patients With DMDtreatment3recruiting
NCT05833633
Study of Genotype and Phenotype Characterization in Duchenne Muscular Dystrophy With Small MutationsNo drug interventionsNot AvailableNot Availablerecruiting
NCT00016653
Creatine and Glutamine in Steroid-Naive Duchenne Muscular Dystrophytreatment2 / 3completed
NCT02286947
Safety Study of Eteplirsen to Treat Advanced Stage Duchenne Muscular Dystrophytreatment2completed
NCT02383511
Modified Diet Trial: A Study of SMT C1100 in Paediatric Patients With DMD Who Follow a Balanced Diettreatment1completed
NCT00018109
A Multicenter Randomized Placebo-Controlled Double-Blind Study to Assess Efficacy and Safety of Glutamine and Creatine Monohydrate in Duchenne Muscular Dystrophy (DMD)treatment3completed
NCT03400852
A Study to Assess the Efficacy and Safety of MNK-1411 in Duchenne Muscular Dystrophytreatment2terminated
NCT02195999
Assessment of Cardiopulmonary Function in Duchenne Muscular DystrophyNo drug interventionsNot AvailableNot Availablecompleted
NCT03769116
A Randomized, Double-blind, Placebo-controlled Study of Delandistrogene Moxeparvovec (SRP-9001) for Duchenne Muscular Dystrophy (DMD)No drug interventionstreatment1 / 2completed
NCT02439216
Phase 1/2 Study in Boys With Duchenne Muscular Dystrophytreatment1 / 2completed
NCT06363357
The Effect of a Muscle-mimicking, Fabric-type Shoulder Orthosis on Functional Movements of the Upper Limb in Patients With Duchenne Muscular DystrophyNo drug interventionssupportive_careNot Availablerecruiting
NCT02369731
Registry of Translarna (Ataluren) in Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD)No drug interventionsNot AvailableNot Availableactive_not_recruiting
NCT00033189
An Open-label Pilot Study of Coenzyme Q10 in Steroid-Treated Duchenne Muscular Dystrophytreatment2completed
NCT00243789
Study of Daily Pentoxifylline as a Rescue Treatment in Duchenne Muscular Dystrophytreatment1 / 2completed
NCT06337669
Characterization of DupEx2 Duchenne Muscular DystrophyNo drug interventionsNot AvailableNot Availablerecruiting
NCT02834650
Validating Cardiac MRI Biomarkers and Genotype-Phenotype Correlations for DMDNo drug interventionsbasic_scienceNot Availablecompleted
NCT01918384
Phase II Study of NPC-14 (Arbekacin Sulfate) to Explore Safety, Tolerability, and Efficacy in Duchenne Muscular Dystrophytreatment2unknown_status
NCT01027884
Phase III Study of Idebenone in Duchenne Muscular Dystrophy (DMD)treatment3completed
NCT01865084
A Study of Tadalafil for Duchenne Muscular Dystrophytreatment3terminated